gene therapy

FDA Lifts Clinical Hold on Solid Biosciences’ DMD Gene Therapy Trial
BioSpace
Thu, 10/1/20 - 11:08 pm
Solid Biosciences
FDA
clinical trials
gene therapy
Duchenne Muscular Dystrophy
CPhl event to draw attention to M&A activity in gene and cell sector
Biopharma Reporter
Thu, 10/1/20 - 10:07 am
M&A
gene therapy
cell therapy
CPhI
New data bolsters Sarepta gene therapies for two deadly muscle diseases
Biopharma Dive
Mon, 09/28/20 - 10:45 am
Sarepta Therapeutics
gene therapy
Duchenne Muscular Dystrophy
Limb Girdle Muscular Dystrophy
SRP-9001
SRP-9003
Pfizer leans into gene therapy manufacturing with 'build-buy-partner' strategy
Fierce Pharma
Thu, 09/24/20 - 10:19 am
Pfizer
gene therapy
Vivet Therapeutics
WIlson's disease
build-buy-partner
FDA sets back Novartis plans to expand use of SMA gene therapy
BioPharma Dive
Wed, 09/23/20 - 10:39 am
Novartis
SMA
gene therapy
Zolgensma
clinical trials
FDA
Epilepsy gene therapy candidate moves closer to clinical study phase
Biopharma Reporter
Thu, 09/17/20 - 10:46 am
CombiGene
Cobra Biologics
CDMOs
gene therapy
epilepsy
CG01
Sarepta faces another gene therapy hiccup as Regenxbio sues over Jim Wilson's patent
Endpoints
Thu, 09/17/20 - 10:40 am
Sarepta Therapeutics
gene therapy
Regenxbio
Duchenne Muscular Dystrophy
Sarepta cites 'overburdened' FDA as factor in DMD gene therapy delay
Fierce Biotech
Fri, 09/11/20 - 10:55 am
Sarepta Therapeutics
Duchenne Muscular Dystrophy
gene therapy
FDA
Rocket Pharmaceuticals receives FDA fast track designation for RP-L401 gene therapy for infantile malignant osteopetrosis
Pharmaceutical Business Review
Fri, 08/28/20 - 10:39 am
Rocket Pharmaceuticals
FDA
fast track
RP-L401
gene therapy
infantile malignant osteopetrosis[]
Astellas' Audentes reports 3rd death in gene therapy trial
Fierce Biotech
Fri, 08/21/20 - 12:11 pm
Audentes Therapeutics
Astellas
clinical trials
gene therapy
patient deaths
AT132
Is valrox dead?
EP Vantage
Thu, 08/20/20 - 11:09 am
Biomarin
hemophilia A
valrox
gene therapy
Roche
Pfizer
FDA
FDA puts up a red light for Passage Bio’s first gene therapy program
Endpoints
Thu, 08/13/20 - 10:44 am
Passage Bio
gene therapy
FDA
Preparing for an influx of cell and gene therapy approvals
Pharmaforum
Mon, 08/3/20 - 10:28 am
FDA
cell therapy
gene therapy
FDA keeps Solid Bio's troubled Duchenne MD gene therapy on clinical lockdown in latest setback
Endpoints
Mon, 07/27/20 - 11:05 am
Solid Biosciences
Duchenne Muscular Dystrophy
FDA
gene therapy
Locanabio’s Combo RNA Modification Platform Targets Multiple RNA Dysfunctions with One Injection
BioSpace
Thu, 07/23/20 - 10:56 am
Locanabio
RNA modification
gene therapy
Forge Bio’s Combo Model for Gene Therapies Attracts $40M in Funding
Xconomy
Tue, 07/21/20 - 10:53 am
Forge Biologics
funding
gene therapy
J&J-partnered MeiraGTx aims at Biogen with new eye gene therapy data
Endpoints
Sat, 07/18/20 - 12:11 pm
JNJ
MeiraGTx
gene therapy
Retinitis pigmentosa
clinical trials
Orchard licenses gene therapy tech from GSK
Fierce Biotech
Wed, 07/15/20 - 11:10 am
Orchard Therapeutics
GSK
stem cells
gene therapy
Biogen boosts gene therapy strategy with Harvard pact focused on inherited eye disease
Fierce Biotech
Mon, 07/6/20 - 12:00 pm
Biogen
gene therapy
eye disease
Harvard
Sarepta bags drug to fully unlock DMD gene therapy opportunity
Fierce Biotech
Thu, 07/2/20 - 11:19 am
Sarepta Therapeutics
Duchenne Muscular Dystrophy
Hansa Biopharma
gene therapy

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