gene therapy

FDA Awards Orphan Drug Designation to Prevail's Gene Therapy for Gaucher Disease
BioSpace
Fri, 02/14/20 - 10:47 am
FDA
Prevail Therapeutics
gene therapy
Gaucher disease
Upcoming events – Avadel takes on Jazz and Axovant awaits early results
EP Vantage
Fri, 02/14/20 - 10:35 am
Avadel
FT218
Jazz Pharmaceuticals
Xyrem
Axovant
gene therapy
Parkinson's Disease
narcolepsy
Novartis faces criticism over Zolgensma ‘health lottery’
PM Live
Thu, 02/6/20 - 11:51 pm
Novartis
SMA
gene therapy
Zolgensma
lottery
Drugmaker BioMarin Seeks New CFO Amid Coming Release Of Potentially Costliest Drug In The World
Forbes
Thu, 02/6/20 - 11:37 pm
Biomarin
valrox
gene therapy
hemophilia A
Catalent laying out $315M to snatch another gene therapy CDMO
Fierce Pharma
Mon, 02/3/20 - 10:39 am
Catalent
gene therapy
Paragon Services
CDMOs
FDA Expects Explosion in Gene Therapy Treatments, Updates Review Policy
Motley Fool
Tue, 01/28/20 - 11:43 pm
FDA
gene therapy
Deerfield vaults to the top of cell and gene therapy CDMO game with $1.1B facility at Philadelphia's newest biopharma hub
Endpoints
Sat, 01/25/20 - 11:27 pm
Deerfield Management
gene therapy
IPOs
CDMOs
Philadelphia
BioMarin sets gene therapy sights beyond hemophilia
BioPharma Dive
Mon, 01/13/20 - 11:40 pm
Biomarin
hemophilia
gene therapy
Generation Bio Pockets $110M for Next Wave of Gene Therapy, IPO Plans
Xconomy
Mon, 01/13/20 - 11:38 pm
gene therapy
IPOs
Generation Bio
Ultragenyx shares jump on 'better than expected' gene therapy data
Fierce Biotech
Fri, 01/10/20 - 10:26 am
Ultragenyx
clinical trials
gene therapy
DTX301
Solid Bio Restructures to Get Halted Gene Therapy Study Back on Track
Xconomy
Thu, 01/9/20 - 10:35 am
Solid Biosciences
gene therapy
reorganization
Duchenne Muscular Dystrophy
3 trends in biotech to watch in 2020
Stat
Mon, 12/30/19 - 10:34 am
IPOs
eteplirsen
CAR-T
gene therapy
cell therapy
biotech
Pharma's gene and cell therapy ambitions will kick into high gear in 2020—despite some major hurdles
Fierce Pharma
Thu, 12/19/19 - 01:11 pm
gene therapy
reimbursement
drug manufacturing
Bristol-Myers Squibb
Pfizer
Biomarin
Sarepta Therapeutics
Gilead Sciences
CAR-T
Zolgensma for free? Yes, but advocates worry about Novartis' lottery-style giveaway
Fierce Pharma
Thu, 12/19/19 - 12:57 pm
Novartis
Zolgensma
SMA
gene therapy
drug pricing
patients
Value-based pricing for gene therapy? Maybe not ready for hemophilia
Biopharma Dive
Thu, 12/12/19 - 10:52 am
Biomarin
hemophilia
hemophilia A
gene therapy
valoctocogene roxaparvovec
uniQure
hemophilia B
etranadez
Hopkins team invents non-viral system for getting gene therapy into cells
Fierce Biotech
Fri, 12/6/19 - 09:29 pm
Johns Hopkins
gene therapy
CRISPR
Limelight Bio emerges with $75m to develop next generation gene therapies to overcome limitations of current treatments
Pharmaceutical Business Review
Fri, 12/6/19 - 10:11 am
LImelight Bio
innovation
gene therapy
FerGene’s Bladder Cancer Phase III Trial Hits Its Mark
BioSpace
Fri, 12/6/19 - 10:09 am
FerGene
gene therapy
bladder cancer
NMIBC
Ferring Pharmaceuticals
Blackstone Life Sciences
clinical trials
Here's Why BioMarin Pharmaceutical Leapt 10.2% in November
Motley Fool
Wed, 12/4/19 - 10:19 am
Biomarin
R&D
gene therapy
Europe
Gene Therapy M&A Appetite Provides Lift After Audentes Deal
Yahoo/Bloomberg
Wed, 12/4/19 - 10:02 am
gene therapy
Astellas
Audentes Therapeutics
M&A
Novartis
Medicines Company

Pages