gene therapy

Biopharmas laid off staffers at least 63 times in Q1: Fierce Biotech analysis
Fierce Biotech
Tue, 04/1/25 - 11:46 am
layoffs
biotech
cell therapy
gene therapy
A recent gene therapy death shines a light on AAV safety
Pharma Voice
Mon, 03/31/25 - 10:10 am
gene therapy
DMD
Sarepta Therapeutics
adeno-associated viruses
Despite raising $1B over past 5 years, ElevateBio lets go of 17% of workforce
Fierce Biotech
Wed, 03/26/25 - 10:16 pm
ElevateBio
layoffs
gene therapy
cell therapy
Gene therapy loses luster as investors eye quicker returns from weight-loss drugs
Yahoo/Reuters
Fri, 03/21/25 - 11:42 am
gene therapy
rare disease
cancer
obesity
weight loss
drug development
Novartis details intrathecal Zolgensma data in bid to reach more SMA patients with gene therapy
Fierce Pharma
Wed, 03/19/25 - 11:25 am
Novartis
Zolgensma
SMA
spinal muscular atrophy
gene therapy
MeiraGTx spins Parkinson’s, obesity gene therapies into AI startup
BioPharma Dive
Thu, 03/13/25 - 11:25 pm
MeiraGTx
Hologen
obesity
gene therapy
Parkinson's Disease
Roche overhauls Spark gene therapy unit, recording $2.4B in full impairment
Fierce Pharma
Mon, 03/10/25 - 11:20 pm
Roche
Spark Therapeutics
gene therapy
restructuring
Regeneron's gene therapy study shows improved hearing in children with congenital deafness
Contemporary Pediatrics
Mon, 02/24/25 - 05:05 pm
Regeneron
gene therapy
DB-OTO
genetic hearing loss
genetic deafness
Pfizer Axes Beqvez Worldwide, Pivoting Away From Gene Therapy for Hemophilia
BioSpace
Fri, 02/21/25 - 10:51 am
Pfizer
Beqvez
gene therapy
hemophila B
Boehringer and partners commence gene therapy trial for cystic fibrosis
Clinical Trials Arena
Fri, 02/21/25 - 10:49 am
Boehringer Ingelheim
gene therapy
cystic fibrosis
clinical trials
Bluebird, at risk of default, agrees to take-private deal
BioPharma Dive
Fri, 02/21/25 - 10:47 am
Bluebird Bio
M&A
Carlyle Group
SK Capital
gene therapy
Solid says early data suggest ‘differentiated’ Duchenne gene therapy
BioPharma Dive
Tue, 02/18/25 - 11:06 pm
Solid Biosciences
gene therapy
Duchenne Muscular Dystrophy
ExpressionEdits and Boehringer Ingelheim partner to optimize gene therapies
Pharmaceutical Business Review
Fri, 02/14/25 - 09:15 am
Boehringer Ingelheim
ExpressionEdits
gene therapy
Astellas shifts investment focus to later-stage opportunities amid reprioritization
Fierce Pharma
Wed, 02/12/25 - 09:23 pm
Astellas
cell therapy
gene therapy
Roche reports positive topline outcomes from DMD treatment trial
Clinical Trials Arena
Tue, 01/28/25 - 10:24 am
Roche
Elevidys
DMD
gene therapy
clinical trials
5 questions facing emerging biotech in 2025
BioPharma Dive
Tue, 01/14/25 - 11:22 am
biotech
funding
China
IPOs
cell therapy
gene therapy
M&A
RegenXBio sells Hunter syndrome gene therapy's U.S., Asia commercial rights for $110M upfront
Fierce Biotech
Tue, 01/14/25 - 09:59 am
Regenxbio
Hunter Syndrome
gene therapy
Asia
Vertex pays Orna $65M to work on next-gen gene therapies for blood disorders
Fierce Biotech
Tue, 01/7/25 - 10:28 am
Vertex Pharmaceuticals
Orna Therapeutics
ReNAgade Therapeutics
gene therapy
sickle cell disease
transfusion-dependent beta thalassemia
Positive data could expand use of Novartis’ gene therapy for SMA
Clinical Trials Arena
Fri, 01/3/25 - 11:02 am
Novartis
gene therapy
SMA
Zolgensma
OAV101 IT
Novartis’ Phase III spinal muscular atrophy therapy trial meets primary endpoint
Clinical Trials Arena
Thu, 01/2/25 - 11:25 am
Novartis
clinical trials
gene therapy
spinal muscular atrophy
SMA
OAV101 IT

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