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gene therapy

FDA shares additional draft guidance on cell and gene therapy

Clinical Trials Arena

Wed, 11/20/24 - 11:20 am

FDA endorses speedy approval path for Regenxbio Duchenne gene therapy

BioPharma Dive

Mon, 11/18/24 - 06:32 pm

CSL Behring shuts down California cell and gene therapy R&D site amid group pivot

Fierce Biotech

Mon, 11/18/24 - 11:27 am

Neurogene falls again on Rett gene therapy side effects

Pharmaphorum

Mon, 11/18/24 - 11:11 am

clinical trials

Neurogene’s stock sinks after adverse event with Rett syndrome gene therapy

Clinical Trials Arena

Tue, 11/12/24 - 10:59 am

clinical trials

Roche Inks Potential $1B Gene Therapy Deal With Dyno, Eyes Neurological Diseases

BioSpace

Thu, 10/24/24 - 08:21 pm

Dyno Therapeutics

neurological disorders

Pfizer lays off 75 more workers in North Carolina in wake of late-stage DMD trial fail

Fierce Pharma

Tue, 10/22/24 - 11:21 pm

MeiraGTx plans to take Parkinson's gene therapy into phase 3

Pharmaphorum

Wed, 10/16/24 - 09:59 am

clinical trials

Parkinson's Disease

Astellas licenses AviadoBio’s dementia gene therapy candidate

Biopharma Reporter

Fri, 10/11/24 - 09:29 am

New data underline cancer risk of Bluebird therapy for brain disease

BioPharma Dive

Thu, 10/10/24 - 11:15 am

Astellas places $2bn+ bet on AviadoBio dementia gene therapy

Pharmaphorum

Tue, 10/8/24 - 09:44 am

frontotemporal dementia

Ultragenyx tweaks gene therapy dosing to dial up efficacy after seeing signs of activity

Fierce Biotech

Fri, 10/4/24 - 09:38 am

Ultragenyx Pharmaceutical

Genespire raises €46.6 million (~$52 million) in a Series B round to advance its first pediatric in-vivo gene therapy into the clinic

Yahoo Finance

Wed, 09/25/24 - 11:58 am

Bluebird bio lays off 25% of workforce as gene therapy pioneer struggles to stay afloat

Fierce Pharma

Tue, 09/24/24 - 11:35 am

4DMT’S Gene Therapy for AMD Clears Phase II, Heads to Late-Stage Studies

BioSpace

Thu, 09/19/24 - 11:07 am

clinical trials

wet age-related macular degeneration

Why some gene therapies face sluggish launches

Medical Marketing and Media

Mon, 09/16/24 - 10:21 pm

Gene therapy startup emerges with green light for first-of-its-kind trial

BioPharma Dive

Thu, 09/12/24 - 11:33 am

adeno-associated viruses

BridgeBio slashes gene therapy budget after early-phase data fall short of 'transformational' target

Fierce Biotech

Wed, 09/11/24 - 11:15 am

clinical trials

Novartis ignites new stage of Voyager pact with $15M capsid deal

Fierce Biotech

Thu, 09/5/24 - 11:28 am

Voyager Therapeutics

Gene therapy biotech Medera looks back to SPAC as way to go public

Fierce Biotech

Thu, 09/5/24 - 11:27 am

cardiovascular disease

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