gene therapy

Takeda and Carmine Enter $900 Million Non-Viral Gene Therapy Collaboration
BioSpace
Wed, 07/1/20 - 10:51 am
Carmine Therapeutics
Takeda
gene therapy
Two patients die in now-halted study of Audentes gene therapy
BioPharma Dive
Sat, 06/27/20 - 11:35 pm
Audentes Therapeutics
gene therapy
patient deaths
clinical trials
AT132
myotubular myopathy
One-and-done gene therapy wipes out Parkinson's symptoms in mouse models
Fierce Biotech
Thu, 06/25/20 - 10:28 am
USCD
Parkinson's Disease
gene therapy
With cell and gene therapy boom coming, experts at Novartis, Kite trumpet need for capacity: panel
Fierce Pharma
Wed, 06/24/20 - 11:21 pm
cell therapy
gene therapy
Novartis
Kite Pharma
Biomarin
Astellas
Sarepta expands gene therapy toolkit, bets $72.5M to hitch a ride on Codiak's exosome tech
Endpoints
Mon, 06/22/20 - 10:26 am
Sarepta Therapeutics
Codiak Biosciences
gene therapy
Pfizer, Sangamo flesh out hemophilia gene therapy data ahead of phase 3
Fierce Biotech
Thu, 06/18/20 - 10:38 am
Pfizer
Sangamo BioSciences
hemophilia A
clinical trials
gene therapy
giroctocogene fitelparvovec
4DMT to Use $75 Million Series C to Advance Three Key Pipeline Products
BioSpace
Tue, 06/16/20 - 06:57 pm
4D Molecular Therapeutics
IPOs
gene therapy
Magenta, Beam partner to explore use of antibody-based conditioning drug for gene therapies
MedCity News
Mon, 06/15/20 - 10:25 am
Magenta Therapeutics
Beam Therapeutics
MGTA-117
gene therapy
sickle cell disease
beta thalassemia
Bit Bio’s “enter button for the keyboard to the software of life” nabs the company $41.5 million
Tech Crunch
Sun, 06/14/20 - 10:40 pm
Bit Bio
startups
drug discovery
gene therapy
New CRISPR, gene therapy results strengthen potential for treatment of blood diseases
BioPharma Dive
Fri, 06/12/20 - 11:11 am
CRISPR
gene therapy
beta thalassemia
sickle cell disease
CRISPR Therapeutics
Vertex
Bluebird Bio
EHA
Scopus Bio preps trials of gene-silencing immuno-oncology drug
Pharmaforum
Fri, 06/12/20 - 10:56 am
Scopus BioPharma
lymphoma
immuno-oncology
CpG-STAT3siRNA
gene therapy
Sarepta, with new data, plans final push for limb-girdle gene therapy
BioPharma Dive
Mon, 06/8/20 - 10:42 am
Sarepta Therapeutics
Limb Girdle Muscular Dystrophy
gene therapy
SRPT-9003
Add ear gene therapy company Akouos to the ever-growing list of IPOs amid Covid-19
Endpoints
Mon, 06/8/20 - 10:26 am
IPOs
Akouos
NASDAQ
gene therapy
hearing loss
BioMarin gene therapy shows sustained benefit in hemophilia A study
Seeking Alpha
Mon, 06/1/20 - 10:42 am
Biomarin
hemophilia A
clinical trials
gene therapy
valoctocogene roxaparvovec
Big gene therapy names line up behind experimental Covid-19 vaccine
Stat
Thu, 05/28/20 - 10:44 am
COVID-19
gene therapy
Novartis
AveXis
What Sanofi Might Buy With Its Regeneron Windfall
Barron's
Wed, 05/27/20 - 11:01 am
Sanofi
Regeneron
M&A
gene therapy
Ultragenyx
Bluebird Bio
New Zolgensma 'inflection point' is here as Novartis snags EU nod for SMA gene therapy
Fierce Pharma
Wed, 05/20/20 - 10:50 am
Novartis
Zolgensma
SMA
spinal muscular atrophy
gene therapy
Europe
Safety questions linger as Pfizer preps Duchenne gene therapy for final test
BioPharma Dive
Fri, 05/15/20 - 10:20 am
Pfizer
gene therapy
Duchenne Muscular Dystrophy
PF-06939926
Thermo Fisher to invest $180M in new gene therapy plant
BioPharma Dive
Wed, 05/13/20 - 10:31 pm
Thermo Fisher
gene therapy
Avrobio posts 22-month update on Fabry gene therapy trial
Fierce Biotech
Wed, 05/13/20 - 11:26 am
Avrbio
Fabry disease
gene therapy
AVR-RD-01

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