Rocket Pharmaceuticals

FDA Rejects Rocket’s Gene Therapy, Cites Need for Additional CMC Info
BioSpace
Sun, 06/30/24 - 10:03 pm
Rocket Pharmaceuticals
FDA
gene therapy
Kresladi.
Rocket gene therapy’s flight to approval delayed by FDA rejection over manufacturing questions
Fierce Biotech
Fri, 06/28/24 - 11:26 am
Rocket Pharmaceuticals
Kresladi
FDA
gene therapy
5 Cell and Gene Therapy Decisions to Watch in 2024
BioSpace
Mon, 04/22/24 - 11:38 am
cell therapy
gene therapy
Pfizer
Beqvez
hemophilia B
Abeona Therapeutics
pz-cel
recessive dystrophic epidermolysis bullosa
Rocket Pharmaceuticals
Kresladi
Leukocyte adhesion deficiency-1
Adaptimmune
afami-cel
advanced synovial sarcoma
Autolus Therapeutics
obe-cel
B cell acute lymphoblastic leukemia
Rocket Pharma gets FDA review extension review of gene therapy
Investing.com
Tue, 02/13/24 - 11:19 pm
Rocket Pharmaceuticals
gene therapy
FDA
Kresladi
Rocket boosted as FDA alignment on pivotal gene therapy trial design sends stock skyward
Fierce Biotech
Wed, 09/13/23 - 11:30 am
Rocket Pharmaceuticals
gene therapy
FDA
clinical trials
RP-A501
Danon disease
Rocket is bringing lenti back
EP Vantage
Wed, 01/4/23 - 09:46 am
lentiviral
Danon disease
Rocket Pharmaceuticals
New pediatric data shoot Rocket's gene therapy toward phase 2, leaving behind FDA concerns
Fierce Biotech
Sun, 10/2/22 - 08:04 pm
Rocket Pharmaceuticals
gene therapy
clinical trials
RP-A501
Rocket inks Renovacor buyout to propel its heart disease gene therapy ambitions
Fierce Biotech
Tue, 09/20/22 - 10:37 am
Rocket Pharmaceuticals
M&A
gene therapy
Renovacor
heart disease
100% overall survival data for gene therapy fuel Rocket for flight to regulators
Fierce Biotech
Fri, 05/20/22 - 10:48 am
Rocket Pharmaceuticals
gene therapy
Leukocyte Adhesion Deficiency-I
FDA lifts clinical hold on Rocket gene therapy trial, creating launchpad for start of pediatric dosing
Fierce Biotech
Mon, 08/16/21 - 11:08 am
Rocket Pharmaceuticals
gene therapy
FDA
Danon disease
Rocket Pharmaceuticals announces buildout of R&D and manufacturing facility to support development of gene therapy pipeline
Pharmaceutical Business Review
Tue, 01/12/21 - 10:54 am
Rocket Pharmaceuticals
drug manufacturing
R&D
New Jersey
Rocket Pharmaceuticals receives FDA fast track designation for RP-L401 gene therapy for infantile malignant osteopetrosis
Pharmaceutical Business Review
Fri, 08/28/20 - 10:39 am
Rocket Pharmaceuticals
FDA
fast track
RP-L401
gene therapy
infantile malignant osteopetrosis[]
Forty Seven, Rocket collaborate on new treatment for Fanconi Anemia
Pharmaceutical Business Review
Thu, 03/12/20 - 11:01 am
Forty Seven
Rocket Pharmaceuticals
R&D
Fanconi Anemia
pediatric
Rocket begins patient dosing in phase 1 trial of RP-A501 in Danon disease
Pharmaceutical Business Review
Wed, 06/19/19 - 09:52 am
Rocket Pharmaceuticals
gene therapy
Danon disease
RP-A501
Follow-on roundup: Acadia raises $275M, Rocket pockets $55M
BioCentury
Thu, 11/29/18 - 12:06 am
Acadia Pharmaceuticals
Rocket Pharmaceuticals
Rocket Pharmaceuticals Releases Preclinical Data for First Investigational Gene Therapy Program for Rare Heart Disorder
CP Wire
Mon, 11/26/18 - 10:01 am
Rocket Pharmaceuticals
RP-A501
Danon disease
Rocket Pharmaceuticals Releases Preclinical Data for First Investigational Gene Therapy Program for Rare Heart Disorder
Mon, 11/26/18 - 09:46 am
Rocket Pharmaceuticals
RP-A501
Danon disease
Rocket Pharmaceuticals' IND for Gene Therapy for Immune Disorder Cleared by FDA
CP Wire
Mon, 11/19/18 - 09:45 am
Rocket Pharmaceuticals
Leukocyte Adhesion Deficiency-I
RP-L201
Rocket Pharmaceuticals' IND for Gene Therapy for Immune Disorder Cleared by FDA
Mon, 11/19/18 - 08:59 am
Rocket Pharmaceuticals
Leukocyte Adhesion Deficiency-I
RP-L201