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» Rocket Pharmaceuticals
Rocket Pharmaceuticals
Rocket boosted as FDA alignment on pivotal gene therapy trial design sends stock skyward
Rocket boosted as FDA alignment on pivotal gene therapy trial design sends stock skyward
Fierce Biotech
Rocket Pharmaceuticals
gene therapy
FDA
clinical trials
RP-A501
Danon disease
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Rocket is bringing lenti back
Rocket is bringing lenti back
EP Vantage
lentiviral
Danon disease
Rocket Pharmaceuticals
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New pediatric data shoot Rocket's gene therapy toward phase 2, leaving behind FDA concerns
New pediatric data shoot Rocket's gene therapy toward phase 2, leaving behind FDA concerns
Fierce Biotech
Rocket Pharmaceuticals
gene therapy
clinical trials
RP-A501
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Rocket inks Renovacor buyout to propel its heart disease gene therapy ambitions
Rocket inks Renovacor buyout to propel its heart disease gene therapy ambitions
Fierce Biotech
Rocket Pharmaceuticals
M&A
gene therapy
Renovacor
heart disease
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100% overall survival data for gene therapy fuel Rocket for flight to regulators
100% overall survival data for gene therapy fuel Rocket for flight to regulators
Fierce Biotech
Rocket Pharmaceuticals
gene therapy
Leukocyte Adhesion Deficiency-I
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FDA lifts clinical hold on Rocket gene therapy trial, creating launchpad for start of pediatric dosing
FDA lifts clinical hold on Rocket gene therapy trial, creating launchpad for start of pediatric dosing
Fierce Biotech
Rocket Pharmaceuticals
gene therapy
FDA
Danon disease
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Rocket Pharmaceuticals announces buildout of R&D and manufacturing facility to support development of gene therapy pipeline
Rocket Pharmaceuticals announces buildout of R&D and manufacturing facility to support development of gene therapy pipeline
Pharmaceutical Business Review
Rocket Pharmaceuticals
drug manufacturing
R&D
New Jersey
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Rocket Pharmaceuticals receives FDA fast track designation for RP-L401 gene therapy for infantile malignant osteopetrosis
Rocket Pharmaceuticals receives FDA fast track designation for RP-L401 gene therapy for infantile malignant osteopetrosis
Pharmaceutical Business Review
Rocket Pharmaceuticals
FDA
fast track
RP-L401
gene therapy
infantile malignant osteopetrosis[]
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Forty Seven, Rocket collaborate on new treatment for Fanconi Anemia
Forty Seven, Rocket collaborate on new treatment for Fanconi Anemia
Pharmaceutical Business Review
Forty Seven
Rocket Pharmaceuticals
R&D
Fanconi Anemia
pediatric
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Rocket begins patient dosing in phase 1 trial of RP-A501 in Danon disease
Rocket begins patient dosing in phase 1 trial of RP-A501 in Danon disease
Pharmaceutical Business Review
Rocket Pharmaceuticals
gene therapy
Danon disease
RP-A501
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Follow-on roundup: Acadia raises $275M, Rocket pockets $55M
Follow-on roundup: Acadia raises $275M, Rocket pockets $55M
BioCentury
Acadia Pharmaceuticals
Rocket Pharmaceuticals
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Rocket Pharmaceuticals Releases Preclinical Data for First Investigational Gene Therapy Program for Rare Heart Disorder
Rocket Pharmaceuticals Releases Preclinical Data for First Investigational Gene Therapy Program for Rare Heart Disorder
CP Wire
Rocket Pharmaceuticals
RP-A501
Danon disease
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Rocket Pharmaceuticals Releases Preclinical Data for First Investigational Gene Therapy Program for Rare Heart Disorder
Rocket Pharmaceuticals
RP-A501
Danon disease
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Rocket Pharmaceuticals' IND for Gene Therapy for Immune Disorder Cleared by FDA
Rocket Pharmaceuticals' IND for Gene Therapy for Immune Disorder Cleared by FDA
CP Wire
Rocket Pharmaceuticals
Leukocyte Adhesion Deficiency-I
RP-L201
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Rocket Pharmaceuticals' IND for Gene Therapy for Immune Disorder Cleared by FDA
Rocket Pharmaceuticals
Leukocyte Adhesion Deficiency-I
RP-L201
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