gene therapy

Novartis and the Gates Foundation aim to create a more practical gene therapy for sickle cell patients around the world
Stat
Wed, 02/17/21 - 10:41 am
Novartis
Gates Foundation
gene therapy
sickle cell disease
Bluebird stops studies of sickle cell gene therapy after new cancer cases
BioPharma Dive
Tue, 02/16/21 - 11:19 am
Bluebird Bio
gene therapy
sickle cell disease
leukemia
clinical trials
A gene therapy pipeline takes shape for a cluster of rare diseases
BioPharma Dive
Mon, 02/15/21 - 11:43 pm
gene therapy
Fabry disease
Avrobio
Biotech entrepreneur George Church launches gene therapy startup to design safer viral vectors
Fierce Biotech
Wed, 02/10/21 - 10:21 pm
George Church
gene therapy
adenovirus
Bayer’s gene therapy juggling act
EP Vantage
Mon, 02/8/21 - 10:35 am
Bayer
gene therapy
AskBio
Avrobio gene therapy eliminates toxic substrate in Fabry patient
Fierce Biotech
Mon, 02/8/21 - 10:26 am
Avrobio
gene therapy
Fabry disease
clinical trials
The diabetes 'cure' Vertex acquired in its 2019 Semma buyout? It's headed to the clinic
Endpoints
Fri, 01/29/21 - 09:54 am
Vertex Pharmaceuticals
Semma Therapeutics
M&A
gene therapy
VX-880
type 1 diabetes
Gene therapy for hemophilia: So close, yet so far away
BioPharma Dive
Thu, 01/28/21 - 11:18 pm
hemophilia
hemophilia A
hemophilia B
gene therapy
Biomarin
uniQure
How 2 scientific pioneers teamed up to run AskBio, Bayer's new gene therapy division
BioPharma Dive
Thu, 01/21/21 - 11:39 pm
Bayer
AskBio
M&A
gene therapy
Rexgenero renamed Ixaka after integration of nanoparticle tech business and funding boost
Biopharma Reporter
Mon, 01/18/21 - 01:22 pm
Rexgenero
cell therapy
Ixaka
nanoparticles
gene therapy
Thermo Fisher Takes Deep Dive into Cell and Gene Therapy with Viral Vector Business Buy
BioSpace
Sat, 01/16/21 - 11:51 pm
Thermo Fisher
cell therapy
gene therapy
viral vector
Henogen AS
BioMarin tries to get hemophilia gene therapy back on track with positive data
BioPharma Dive
Mon, 01/11/21 - 10:40 am
Biomarin
hemophilia A
gene therapy
clinical trials
Roctavian
Pfizer beats Sarepta to the start of first late-stage Duchenne gene therapy trial
BioPharma Dive
Thu, 01/7/21 - 11:36 am
Pfizer
Sarepta Therapeutics
clinical trials
Duchenne Muscular Dystrophy
gene therapy
Biotech Bayer's VC arm leads $105M round for 'gene circuit' startup Senti Bio
Fierce Biotech
Wed, 01/6/21 - 11:05 pm
Bayer
venture capital
gene therapy
Senti Biosciences
Fujifilm's CDMO carves foothold in Boston biotech hub with new HQ focused on viral vectors, gene therapies
Endpoints
Tue, 01/5/21 - 10:22 am
Fujifilm
Fujifilm Diosynth Biotechnologies
CDMOs
Boston
gene therapy
vaccines
Audentes sees FDA hold lifted after 3 trial deaths blighted $3B program
Fierce Biotech
Mon, 12/28/20 - 10:59 am
Audentes
Astellas
FDA
clinical trials
AT132
gene therapy
X-linked myotubular myopathy
UniQure/CSL hit by FDA clinical hold for hem B gene therapy program after liver cancer find
Fierce Biotech
Mon, 12/21/20 - 11:09 am
uniQure
CSL
FDA
clinical trials
hemophilia B
gene therapy
etranacogene dezaparvovec
Bluebird trumpets long-term data from beta-thalassaemia gene therapy
Pharmaforum
Wed, 12/9/20 - 10:40 am
Bluebird Bio
Zinteglo
gene therapy
beta-thalassemia
#ASH20 Best of the Rest: Pfizer, Sangamo launch a durability charge at BioMarin in hem A; The data behind Merck's $4.5B buyout
Endpoints
Mon, 12/7/20 - 10:32 am
ASH2020
uniQure
hemophilia A
Sangamao
gene therapy
Biomarin
Janssen buys up eye disorder gene therapy asset from Hemera Biosciences
Fierce Biotech
Wed, 12/2/20 - 10:45 am
Janssen
JNJ
Hemera Biosciences
gene therapy
HMR59
geographic atrophy

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