You are here

gene therapy

Sarepta's second-gen Duchenne drug shows signs of topping its first

BioPharma Dive

Mon, 05/3/21 - 10:54 pm

Sarepta Therapeutics

Duchenne Muscular Dystrophy

Epidermolysis bullosa gene therapies wait in the wings

EP Vantage

Thu, 04/29/21 - 10:50 am

epidermolysis bullosa

Adverum gene therapy trial sees disruption after serious side effect reported

Biopharma Reporter

Thu, 04/29/21 - 10:39 am

Adverum Biotechnologies

diabetic macular edema

clinical trials

Astellas takes $540M impairment charge over Audentes' gene therapy trial hold

Fierce Biotech

Tue, 04/27/21 - 10:47 am

FDA says Voyager can trek on as it removes trial hold for Huntington's gene therapy test

Fierce Biotech

Mon, 04/26/21 - 11:15 am

Voyager Therapeutics

Huntington's disease

FDA lifts clinical hold on uniQure's gene therapy amid cancer concerns; shares jump

Fierce Biotech

Mon, 04/26/21 - 12:06 pm

Bayer plots a major facelift at Berkeley campus, uncorking a 30-year, $1.2B plan to drive cell and gene therapies

Endpoints

Thu, 04/22/21 - 11:29 pm

Bluebird bio lays off staffers in Europe as Zynteglo rollout hits an early reimbursement snag

Fierce Pharma

Tue, 04/20/21 - 07:38 pm

Avrobio is using 'pods' to create gene therapies, and it believes the approach could change the game altogether

Endpoints

Fri, 04/16/21 - 12:01 am

drug manufacturing

Nearly a year after Audentes' gene therapy deaths, the trial continues. What happened remains a mystery

Endpoints

Wed, 04/14/21 - 09:37 am

clinical trials

Senti Biosciences in $645M Spark pact to drive gene circuits into the fast lane

Fierce Biotech

Wed, 04/14/21 - 09:34 am

Spark Therapeutics

Senti Biosciences

Cell and gene therapy services market forecast to see significant growth over the next decade

Biopharma Reporter

Mon, 04/12/21 - 10:44 am

clinical trials

Audentes CEO exits as Astellas rebrands a gene therapy buyout

BioPharma Dive

Thu, 04/1/21 - 11:01 am

Astellas Gene Therapies

Astellas gene therapy repairs damage in neurodegenerative disease models

Fierce Biotech

Wed, 03/31/21 - 11:08 pm

neurodegenerative disease

Uniqure's Hemophilia B Gene Therapy Unlikely To Be Cause Of Liver Cancer Reported In One Patient

Benzinga

Mon, 03/29/21 - 10:36 am

etranacogene dezaparvovec

clinical trials

Gyroscope bags $148M for AMD gene therapy trials, mulls IPO

Fierce Biotech

Fri, 03/26/21 - 10:53 am

age-related macular degeneration

Novartis is shutting down Colorado plant, laying off 400 employees after overestimating gene therapy demand

Fierce Pharma

Thu, 03/25/21 - 11:18 am

drug manufacturing

XyloCor bags $23M to expand heart disease gene therapy R&D

Fierce Biotech

Mon, 03/22/21 - 10:46 am

XyloCor Therapeutics

clinical trials

With new results, Sarepta's 2nd gene therapy holds steady

BioPharma Dive

Sun, 03/21/21 - 11:46 pm

Sarepta Therapeutics

limb-girdle muscular dystrophy

Record funding flowed into cell, gene therapy companies last year

BioPharma Dive

Tue, 03/16/21 - 10:42 pm

Pages