hemophilia A

BioMarin Narrows Roctavian Efforts to U.S., Germany, Italy as Sales Stagnate
BioSpace
Tue, 08/6/24 - 11:23 am
Biomarin
Roctavian
hemophilia A
Germany
Italy
Despite Late-Stage Hemophilia Win, Sangamo Remains in Do-or-Die Situation
BioSpace
Wed, 07/31/24 - 10:48 am
Sangamo BioSciences
Pfizer
hemophilia A
gene therapy
Pfizer says hemophilia gene therapy meets late-stage study goal
BioPharma Dive
Wed, 07/24/24 - 11:53 am
Pfizer
gene therapy
hemophilia A
clinical trials
giroctocogene fitelparvovec
Novo Nordisk unwraps phase 3 hemophilia A data, revealing how Roche rivalry may shake out
Fierce Biotech
Mon, 06/24/24 - 10:54 am
Novo Nordisk
Mim8
hemophilia A
clinical trials
Roche
Hemlibra
Novo Nordisk's Hemophilia Candidate Can Prevent Bleeding Episodes Effectively, Regardless Of Dosing Frequency
Yahoo/Benzinga
Mon, 05/13/24 - 10:11 pm
Novo Nordisk
clinical trials
hemophilia A
Mim8
Roche’s Hemlibra shows benefit in Phase III hemophilia A trial
Clinical Trials Arena
Mon, 12/11/23 - 09:57 am
Roche
Hemlibra
hemophilia A
clinical trials
With Roctavian as a launching pad, BioMarin looks to up pace of new drug filings
Fierce Biotech
Tue, 09/12/23 - 07:17 pm
Biomarin
Roctavian
hemophilia A
Voxzogo
achrondoplasia
drug development
gene therapy
Voxzogo saves the day for Biomarin
EP Vantage
Tue, 08/1/23 - 10:05 am
Biomarin
hemophilia A
gene therapy
Roctavian
Voxzogo
Roche Drops Hemophilia A Candidate, Prepares for the Impacts of IRA
BioSpace
Thu, 07/27/23 - 11:36 am
Roche
RG6358
Spark Therapeutics
hemophilia A
earnings
BioMarin's hemophilia gene therapy Roctavian lands FDA nod with 'glimmers' of enthusiasm among doctors
Fierce Pharma
Thu, 06/29/23 - 10:56 pm
BioMarin Pharmaceuticall
Roctavian
FDA
hemophilia A
gene therapy
After Hemgenix approvals, uniQure cashes out some of its royalty rights for $375M-plus
Fierce Pharma
Mon, 05/15/23 - 06:23 pm
uniQure
Hemgenix
gene therapy
hemophilia A
FDA delays review of BioMarin's hemophilia gene therapy after data update
Endpoints
Tue, 03/7/23 - 11:16 am
Biomarin
gene therapy
hemophilia A
FDA
valrox
Sanofi’s clinical trial of hemophilia A therapy in children meets endpoint
Clinical Trials Arena
Sun, 03/5/23 - 03:12 pm
Sanofi
clinical trials
hemophilia A
Altuviiio
FDA approves Sanofi’s long-lasting hemophilia drug
BioPharma Dive
Thu, 02/23/23 - 04:32 pm
Sanofi
FDA
hemophilia A
Altuviiio
Sanofi dives deeper into phase 3 data for Hemlibra rival as FDA decision approaches
Fierce Biotech
Thu, 01/26/23 - 10:47 am
Sanofi
FDA
clinical trials
hemophilia A
efanesoctocog alfa
Roche
Hemlibra
5 FDA decisions to watch in the first quarter
BioPharma Dive
Mon, 01/9/23 - 10:27 am
FDA
Eli Lilly
donanemab
Alzheimer's disease
Menareni
Elacestrant
breast cancer
Biomarin
Roctavian
hemophilia A
Acadia Pharmaceuticals
trofinetide
Rett Syndrome
Gilead Sciences
Trodelvy
BioMarin gets FDA decision date for hemophilia gene therapy, but questions on review remain
BioPharma Dive
Thu, 10/13/22 - 11:52 pm
Biomarin
FDA
hemophilia A
gene therapy
Roctavian
BioMarin Banks on More Robust Data in Hemophilia A Resubmission
BioSpace
Fri, 09/30/22 - 10:59 am
Biomarin
FDA
hemophilia A
valoctocogene roxaparvovec
Months after exiting clinical hold, Pfizer readies to resume dosing in phase 3 gene therapy trial
Fierce Biotech
Fri, 09/23/22 - 10:50 am
Pfizer
clinical trials
hemophilia A
gene therapy
FDA
giroctocogene fitelparvovec
BioMarin says PhIII gene therapy study participant's cancer is unrelated to therapy
Endpoints
Mon, 09/12/22 - 11:42 pm
Biomarin
gene therapy
hemophilia A
clinical trials

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