gene therapy

Ginkgo grows its gene therapy offerings with StrideBio deal
BioPharma Dive
Wed, 04/5/23 - 07:09 pm
Ginkgo Bioworks
StrideBio
gene therapy
FDA grants orphan drug designation to HuidaGene gene therapy for blindness
Pharmaceutical Business Review
Tue, 04/4/23 - 12:25 pm
HuidaGene
HG004
gene therapy
FDA
retinal disease
Pharma partner Sartorius eyes gene therapy market with $2.6B deal
BioPharma Dive
Sun, 04/2/23 - 04:29 pm
gene therapy
Sartorius
Polyplus
Gene therapy startup Vedere to close two years after launch
BioPharma Dive
Sun, 04/2/23 - 04:20 pm
Vedere Bio
Novartis
gene therapy
Nanoscope’s eye disease gene therapy shows mixed results in PhII
Endpoints
Fri, 03/31/23 - 10:35 am
Nanoscope Therapeutics
gene therapy
MCO-010
Bluebird to miss Q1 deadline for lovo-cel filing, shares sliced
Endpoints
Wed, 03/29/23 - 04:04 pm
Bluebird Bio
sickle cell disease
gene therapy
FDA
lovo-cel
Moderna's gene therapy expansion picks up pace with $76M upfront Generation Bio collab
Fierce Biotech
Thu, 03/23/23 - 11:53 am
Moderna Therapeutics
gene therapy
Generation Bio
FDA's Peter Marks backs accelerated approval for gene therapies
BioSpace
Tue, 03/21/23 - 11:36 am
FDA
CDER
Peter Marks
gene therapy
accelerated approval
Novartis: SMA Drug Zolgensma Long-term Data Shows Sustained Durability Up To 7.5 Years Post-dosing
NASDAQ
Mon, 03/20/23 - 04:47 pm
Novartis
SMA
Zolgensma
gene therapy
FDA Reverses Course; Will Hold Adcomm for Sarepta’s DMD Gene Therapy
BioSpace
Fri, 03/17/23 - 10:13 am
FDA
Sarepta Therapeutics
DMD
gene therapy
Duchenne Muscular Dystrophy
SRP-9001
Duchenne muscular dystrophy: major trials and events to watch in 2023
Clinical Trials Arena
Thu, 03/16/23 - 09:49 am
DMD
Duchenne Muscular Dystrophy
clinical trials
gene therapy
FDA
Sarepta Therapeutics
SRP-9001
FibroGen
pamrevlumab
Capricor
CAP-1002
Santhera
ReveraGen
vamorolone
CRISPR/ViaCyte and Genprex Vie for First Diabetes Gene Therapy
BioSpace
Mon, 03/13/23 - 10:21 am
ViaCyte
CRISPR Therapeutics
Genprex
diabetes
gene therapy
FDA delays review of BioMarin's hemophilia gene therapy after data update
Endpoints
Tue, 03/7/23 - 11:16 am
Biomarin
gene therapy
hemophilia A
FDA
valrox
Sarepta: FDA finds ‘no significant safety issues of concern’ with DMD gene therapy
Biopharma Reporter
Mon, 03/6/23 - 11:29 pm
Sarepta Therapeutics
DMD
Duchenne Muscular Dystrophy
gene therapy
FDA
Sangamo scraps public offering ‘after evaluating market conditions’
Endpoints
Sun, 03/5/23 - 03:28 pm
Sangamo
stock offering
cell therapy
gene therapy
Spark Breaks Ground on Gene Therapy Innovation Center on Drexel Campus in Philadelphia
BioBuzz
Thu, 03/2/23 - 10:10 am
Spark Therapeutics
gene therapy
Philadelphia
Drexel University
CBER director Peter Marks says FDA is growing to keep up with cell and gene therapies
Endpoints
Wed, 03/1/23 - 06:50 pm
CBER
Peter Marks
FDA
gene therapy
cell therapy
Sarepta's DMD gene therapy inches closer to market as FDA declines to hold advisory meeting
Fierce Biotech
Wed, 03/1/23 - 09:52 am
FDA
Sarepta Therapeutics
SRP-9001
gene therapy
DMD
Duchenne Muscular Dystrophy
FDA plans to launch communications pilot for promising rare disease gene therapies
RAPS.org
Mon, 02/27/23 - 07:10 pm
FDA
biologics
gene therapy
Rare Diseases
regulatory
AbbVie, Capsida Set Sights on Gene Therapies for Eye Diseases
BioSpace
Thu, 02/23/23 - 10:02 am
AbbVie
Capsida Biotherapeutics
gene therapy
eye disease

Pages