gene therapy

Lilly makes waves, says gene therapy restores hearing for child with genetic hearing loss
Fierce Biotech
Tue, 01/23/24 - 06:04 pm
Eli Lilly
gene therapy
hearing loss
Akouos
AK-OTOF
Sickle Cell Gene Therapies Seen as Cost Effective Below $2M Threshold: Study
BioSpace
Tue, 01/23/24 - 11:18 am
gene therapy
sickle cell disease
drug pricing
Vertex Pharmaceuticals
Bluebird Bio
Roche's Genentech spends $15M to rocket into GenEdit’s NanoGalaxy
Fierce Biotech
Tue, 01/23/24 - 10:43 am
Roche
Genentech
GenEdit
drug development
gene therapy
autoimmune disease
FDA’s Marks Advocates for Flexibility in Rare Disease Gene Therapy Trials
BioSpace
Mon, 01/22/24 - 11:01 am
FDA
regulatory
Peter Marks
CBER
clinical trials
gene therapy
Sensorion gets go ahead to launch hearing loss gene therapy trial
Clinical Trials Arena
Sun, 01/21/24 - 04:56 pm
Sensorion
clinical trials
gene therapy
SENS-501
CAR-T hype faces infrastructure reality check
Fierce Pharma
Tue, 01/16/24 - 09:22 am
CAR-T
cell therapy
gene therapy
Gilead Sciences
JNJ
Gene Therapy Approvals Expected to Ramp Up in 2024 Amid Manufacturing, Cost Challenges
BioSpace
Tue, 01/9/24 - 10:24 am
gene therapy
cell therapy
FDA
Bluebird bio's Lyfgenia launch progresses with 2nd major outcomes-based coverage deal
Fierce Pharma
Thu, 01/4/24 - 11:37 am
Bluebird Bio
Lyfgenia
sickle cell disease
gene therapy
Genascence begins Phase Ib gene therapy trial for knee osteoarthritis
Clinical Trials Arena
Thu, 01/4/24 - 10:14 am
Genascence
clinical trials
GNSC-001
gene therapy
osteoarthritis of the knee
Bayer's AskBio checks off another early win for gene therapy platform with Parkinson's safety data
Fierce Biotech
Thu, 01/4/24 - 10:12 am
Bayer
AskBio
gene therapy
Parkinson's Disease
Pfizer rings in New Year with hemophilia B gene therapy nod in Canada
Fierce Pharma
Wed, 01/3/24 - 05:10 pm
Pfizer
Canada
gene therapy
hemophilia B
Beqvez
With trial win for oral thalassemia drug, Agios charts broader path than gene therapy rivals
Fierce Pharma
Wed, 01/3/24 - 05:01 pm
Agios Pharmaceuticals
mitapivat
beta thalassemia
gene therapy
Novartis, Voyager launch another gene therapy mission with $100M upfront deal
Fierce Biotech
Tue, 01/2/24 - 10:05 am
Novartis
gene therapy
Voyager Therapeutics
Huntington's disease
SMA
Takeda’s gene therapy pivot leaves JCR behind after proof-of-concept preclinical test
Fierce Biotech
Thu, 12/21/23 - 09:57 am
Takeda
gene therapy
JCR Pharma
Benefit of uniQure's Huntington's gene therapy will be revealed 'in the fullness of time'
Fierce Biotech
Tue, 12/19/23 - 11:14 pm
uniQure
Huntington's disease
gene therapy
Bluebird’s Newly Approved SCD Gene Therapy Faces Rough Road with Hefty Price Tag, Boxed Warning
BioSpace
Mon, 12/11/23 - 11:20 am
Bluebird Bio
sickle cell disease
Lyfgenia
gene therapy
CRISPR
Sen. Bill Cassidy Eyes Legislation to Improve Access to Gene Therapies
BioSpace
Wed, 12/6/23 - 10:26 am
Senate
legislation
gene therapy
patient access
BioMarin secures hemophilia gene therapy coverage in Germany
BioPharma Dive
Wed, 11/29/23 - 11:35 pm
Biomarin
Roctavian
gene therapy
Germany
hemophilia
Cell & Gene Therapy Space Gears Up for First CRISPR Approval
BioSpace
Mon, 11/13/23 - 11:48 am
CRISPR
gene therapy
cell therapy
sickle cell disease
exa-cel
Vertex Pharmaceuticals
CRISPR Therapeutics
Bayer adds a new life science incubator in China
Pharmaphorum
Tue, 11/7/23 - 10:04 am
Bayer
Co.Lab
incubators
China
oncology
cell therapy
gene therapy

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