DMD

Wave surfs DMD success to regulators' doors, sending stock up
Fierce Biotech
Tue, 09/24/24 - 11:45 am
Wave Life Sciences
DMD
Duchenne Muscular Dystrophy
clinical trials
FDA designations boost AI-Driven cell therapy approach for Duchenne muscular dystrophy
Biopharma Reporter
Tue, 09/17/24 - 09:53 am
Somite
FDA
pediatrics
cell replacement therapy
artificial intelligence
DMD
Duchenne Muscular Dystrophy
Three execs resign as Dyne posts mixed data for DMD candidate
Fierce Biotech
Tue, 09/3/24 - 05:56 pm
Dyne Therapeutics
DMD
DYNE-251
DMD clinical studies evolve with emphasis on building designs around relevant endpoints
Clinical Trials Arena
Fri, 08/30/24 - 11:24 am
DMD
Duchenne Muscular Dystrophy
clinical trials
Satellos to commence Phase I trial for DMD drug
Clinical Trials Arena
Thu, 08/8/24 - 11:18 am
Satellos Bioscience
DMD
clinical trials
SAT-3247
In a Duchenne market beset by problems, Capricor data marks a bright spot
Pharma Voice
Mon, 08/5/24 - 11:04 am
Capricor
CAP-1002
deramiocel
DMD
Sanofi sues Sarepta, claiming Duchenne gene therapy Elevidys infringes 2 manufacturing patents
Fierce Pharma
Tue, 07/30/24 - 06:35 pm
Sarepta Therapeutics
Sanofi
legal
patents
Elevidys
DMD
Pfizer takes $230M hit after axing failed DMD gene therapy—and tosses out RSV combo vaccine
Fierce Biotech
Tue, 07/30/24 - 11:50 am
Pfizer
DMD
gene therapy
RSV
Capricor’s cell therapy shows three year benefit in DMD patients
Clinical Trials Arena
Mon, 07/1/24 - 11:13 am
Capricor
deramiocel
cell therapy
DMD
clinical trials
After full approval, Sarepta lays out its next moves
BioSpace
Wed, 06/26/24 - 11:31 am
Sarepta Therapeutics
DMD
Elevidys
gene therapy
Sarepta Duchenne gene therapy wins broader use from FDA
BioPharma Dive
Thu, 06/20/24 - 06:09 pm
Sarepta Therapeutics
gene therapy
FDA
DMD
Elevidys
Pfizer setback brings questions for Duchenne gene therapy ahead of Sarepta decision
BioPharma Dive
Thu, 06/13/24 - 11:07 pm
Pfizer
DMD
gene therapy
FDA
Sarepta Therapeutics
Elevidys
Pfizer gene therapy for Duchenne fails to meet goals of key trial
BioPharma Dive
Wed, 06/12/24 - 11:32 pm
Pfizer
Duchenne Muscular Dystrophy
DMD
clinical trials
Ciffreo
Nippon Shinyaku’s DMD drug fails confirmatory trial
Pharmaphorum
Tue, 05/28/24 - 10:42 am
Nippon Shinyaku
DMD
Viltepso
clinical trials
Sarepta Seeks Label Expansion, Bigger Market for DMD Gene Therapy
BioSpace
Wed, 05/8/24 - 11:13 am
Sarepta Therapeutics
DMD
Elevidys
gene therapy
Patient dies in Pfizer study of Duchenne gene therapy
BioPharma Dive
Tue, 05/7/24 - 06:32 pm
Pfizer
DMD
fordadistrogene movaparvovec
clinical trials
patient deaths
5 DMD Data Readouts to Watch in 2024
BioSpace
Mon, 05/6/24 - 11:24 am
DMD
clinical trials
Pfizer
gene therapy
fordadistrogene movaparvovec
Dyne Therapeutics
DYNE-251
Edgewise Therapeutics
EDG-5506
Capricor
CAP-1002
Avidity Biosciences
AOC 1044
FDA’s Accelerated Approval of Sarepta DMD Gene Therapy Comes Under Fire
BioSpace
Fri, 05/3/24 - 11:20 am
FDA
accelerated approvals
Sarepta Therapeutics
DMD
gene therapy
FDA approves Italfarmaco’s Duvyzat for DMD treatment
Pharmaceutical Business Review
Fri, 03/22/24 - 09:38 am
Italfarmaco
FDA
Duvyzat
DMD
Duchenne Muscular Dystrophy
Regenxbio data suggest ‘niche’ in Duchenne gene therapy
BioPharma Dive
Thu, 03/7/24 - 11:05 am
Regenxbio
Duchenne Muscular Dystrophy
DMD
RGX-202
Sarepta Therapeutics
Elevidys

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