gene therapy

Sarepta's DMD gene therapy inches closer to market as FDA declines to hold advisory meeting
Fierce Biotech
Wed, 03/1/23 - 09:52 am
FDA
Sarepta Therapeutics
SRP-9001
gene therapy
DMD
Duchenne Muscular Dystrophy
FDA plans to launch communications pilot for promising rare disease gene therapies
RAPS.org
Mon, 02/27/23 - 07:10 pm
FDA
biologics
gene therapy
Rare Diseases
regulatory
AbbVie, Capsida Set Sights on Gene Therapies for Eye Diseases
BioSpace
Thu, 02/23/23 - 10:02 am
AbbVie
Capsida Biotherapeutics
gene therapy
eye disease
First Gene Therapy for Hemophilia B, CSL's HEMGENIX®, Approved by the European Commission
BioSpace
Tue, 02/21/23 - 10:00 am
CSL
Europe
Hemgenix
gene therapy
hemophilia B
'It's the right call': GSK expresses no regrets on abandoning cell therapy as oligo strategy heats up
Fierce Biotech
Fri, 02/17/23 - 09:46 am
GSK
cell therapy
gene therapy
oligonucleotides
Wave Life Sciences
A renewed push into early bladder cancer
EP Vantage
Thu, 02/2/23 - 10:24 am
Ferring Pharmaceuticals
Adstiladrin
FDA
gene therapy
bladder cancer
Taysha’s GAN Gene Therapy Hits FDA Speedbump
BioSpace
Wed, 02/1/23 - 10:35 am
Taysha Gene Therapies
TSHA-120
axonal neuropathy
clinical trials
gene therapy
FDA
Amid application tsunami, FDA's top cell and gene therapy leader to retire in March
Endpoints
Tue, 01/31/23 - 11:09 pm
FDA
gene therapy
cell therapy
UniQure nabs another gene therapy for ALS
BioPharma Dive
Tue, 01/31/23 - 12:34 pm
UniQuire
Apic Bio
ALS
gene therapy
AMT-162
A startup launches with plans to open up a gene and cell therapy bottleneck
BioPharma Dive
Tue, 01/31/23 - 10:32 am
Vector BioMed
cell therapy
gene therapy
startups
vectors
XyloCor wraps up PhII for heart disease gene therapy, plans for pivotal trial
Endpoints
Fri, 01/27/23 - 10:31 am
XyloCor Therapeutics
gene therapy
heart disease
clinical trials
Sales of J&J, Legend cell therapy plateau amid production challenges
BioPharma Dive
Wed, 01/25/23 - 10:57 pm
JNJ
Legend Biotech
gene therapy
Carvykti
Multiple Myeloma
Promising gene therapy delivers treatment directly to brain
Stat
Tue, 01/24/23 - 06:11 pm
gene therapy
brain
drug delivery
PTC Therapeutics
Trends Impacting Medtech & Biotech Job Markets in 2023
Medical Devices and Diagnostics Industry
Mon, 01/23/23 - 11:05 am
biotech
Medtech
job market
cell therapy
gene therapy
data
security
benefits
Astellas, after years of gene therapy woes, gets rare boost with FDA lifting of Pompe clinical hold
Fierce Biotech
Fri, 01/20/23 - 10:24 am
Astellas
Pompe disease
gene therapy
AT845
EMA weighs new safety guidance for Novartis’ gene therapy Zolgensma
BioPharma Dive
Tue, 01/17/23 - 10:26 am
Novartis
gene therapy
Zolgensma
SMA
Europe
JPM2023: Breakthroughs await, but so do roadblocks
Pharmaphorum
Fri, 01/13/23 - 10:09 am
JPMHC 2023
Inflation Reduction Act
cell therapy
gene therapy
clinical trials
CNS disorders
Pfizer pivots from early-stage rare disease R&D, shifting to external innovation and putting assets up for sale
Fierce Biotech
Fri, 01/6/23 - 10:09 am
Pfizer
R&D
externalization
gene therapy
Rare Diseases
Sarepta marches forward with its potential DMD gene therapy and an expanded Catalent manufacturing deal
Endpoints
Thu, 01/5/23 - 04:58 pm
Sarepta Therapeutics
SRP-9001
gene therapy
Duchenne Muscular Dystrophy
CDMOs
Catalent
Lilly's Prevail, Capsida partner to develop gene therapies for nervous system diseases
BioPharma Dive
Wed, 01/4/23 - 05:32 pm
Eli Lilly
gene therapy
Capsida
CNS disorders
Prevail Therapeutics

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