gene therapy

Gene & cell therapy manufacturer Ascend launches with more than $130M
Labiotech.eu
Tue, 05/9/23 - 12:20 pm
Ascend Gene & Cell Therapies
gene therapy
drug manufacturing
Life Bio, Forge to develop gene therapies for aging-linked diseases
Pharmaceutical Business Review
Tue, 05/9/23 - 10:41 am
Life Biosciences
Forge Biologics
gene therapy
cGMP manufacturing
Gene Therapies Are Still Hampered By Substantial Delays Between Approval And Launch
Forbes
Wed, 05/3/23 - 11:48 am
gene therapy
drug approvals
Biomarin
Bluebird Bio
FDA
Go or no go? Sarepta’s gene therapy faces scrutiny
EP Vantage
Thu, 04/27/23 - 10:29 am
Sarepta Therapeutics
gene therapy
SRP-9001
Roche
DMD
Duchenne Muscular Dystrophy
Busy with 3 program launches this year, Biogen trims pipeline
Fierce Biotech
Tue, 04/25/23 - 11:40 am
Biogen
stroke
gene therapy
ophthalmology
earnings
Sarepta shares drop as report says FDA almost rejected under-review gene therapy
Yahoo/Reuters
Fri, 04/14/23 - 10:16 am
Sarepta Therapeutics
FDA
gene therapy
DMD
Duchenne Muscular Dystrophy
Vertex/CRISPR's gene editing therapy cost effective at $1.9 million - pricing review group
Yahoo/Reuters
Thu, 04/13/23 - 10:01 am
Vertex Pharmaceutials
CRISPR Therapeutics
gene therapy
sickle cell disease
ICER
A new biotech wants to ease a bottleneck in cell and gene therapy production
BioPharma Dive
Tue, 04/11/23 - 07:28 pm
cell therapy
gene therapy
VintaBio
Layoffs loom as Takeda trims early-stage efforts in AAV gene therapy, rare hematology
Fierce Biotech
Fri, 04/7/23 - 01:45 pm
Takeda
R&D
gene therapy
hematology
'Like salmon swimming upstream': FDA's Peter Marks lays out plan to boost gene therapy approvals
Fierce Biotech
Wed, 04/5/23 - 07:13 pm
FDA
gene therapy
Peter Marks
Ginkgo grows its gene therapy offerings with StrideBio deal
BioPharma Dive
Wed, 04/5/23 - 07:09 pm
Ginkgo Bioworks
StrideBio
gene therapy
FDA grants orphan drug designation to HuidaGene gene therapy for blindness
Pharmaceutical Business Review
Tue, 04/4/23 - 12:25 pm
HuidaGene
HG004
gene therapy
FDA
retinal disease
Pharma partner Sartorius eyes gene therapy market with $2.6B deal
BioPharma Dive
Sun, 04/2/23 - 04:29 pm
gene therapy
Sartorius
Polyplus
Gene therapy startup Vedere to close two years after launch
BioPharma Dive
Sun, 04/2/23 - 04:20 pm
Vedere Bio
Novartis
gene therapy
Nanoscope’s eye disease gene therapy shows mixed results in PhII
Endpoints
Fri, 03/31/23 - 10:35 am
Nanoscope Therapeutics
gene therapy
MCO-010
Bluebird to miss Q1 deadline for lovo-cel filing, shares sliced
Endpoints
Wed, 03/29/23 - 04:04 pm
Bluebird Bio
sickle cell disease
gene therapy
FDA
lovo-cel
Moderna's gene therapy expansion picks up pace with $76M upfront Generation Bio collab
Fierce Biotech
Thu, 03/23/23 - 11:53 am
Moderna Therapeutics
gene therapy
Generation Bio
FDA's Peter Marks backs accelerated approval for gene therapies
BioSpace
Tue, 03/21/23 - 11:36 am
FDA
CDER
Peter Marks
gene therapy
accelerated approval
Novartis: SMA Drug Zolgensma Long-term Data Shows Sustained Durability Up To 7.5 Years Post-dosing
NASDAQ
Mon, 03/20/23 - 04:47 pm
Novartis
SMA
Zolgensma
gene therapy
FDA Reverses Course; Will Hold Adcomm for Sarepta’s DMD Gene Therapy
BioSpace
Fri, 03/17/23 - 10:13 am
FDA
Sarepta Therapeutics
DMD
gene therapy
Duchenne Muscular Dystrophy
SRP-9001

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