gene therapy

After full approval, Sarepta lays out its next moves
BioSpace
Wed, 06/26/24 - 11:31 am
Sarepta Therapeutics
DMD
Elevidys
gene therapy
Sarepta Duchenne gene therapy wins broader use from FDA
BioPharma Dive
Thu, 06/20/24 - 06:09 pm
Sarepta Therapeutics
gene therapy
FDA
DMD
Elevidys
Pfizer setback brings questions for Duchenne gene therapy ahead of Sarepta decision
BioPharma Dive
Thu, 06/13/24 - 11:07 pm
Pfizer
DMD
gene therapy
FDA
Sarepta Therapeutics
Elevidys
Regenxbio CEO to step down after 15 years
BioPharma Dive
Wed, 06/12/24 - 11:23 pm
Regenxbio
Pharma CEOs
gene therapy
Kenneth Mills
Merck KGaA to buy gene therapy tools maker for $600M
BioPharma Dive
Thu, 05/23/24 - 09:37 pm
Merck KGaA
M&A
MilliporeSigma
Gamma Biosciences
gene therapy
Cell and Gene Therapies Still Have Long Way to Go in Fulfilling Promise
BioSpace
Fri, 05/10/24 - 11:39 am
ASGCT
cell therapy
gene therapy
Bluebird Boasts Nearly 140% Revenue Jump, Still Misses Target
BioSpace
Fri, 05/10/24 - 11:10 am
Bluebird Bio
earnings
gene therapy
In gene therapy race, bluebird leads Vertex in activating treatment centers but trails in patient starts
Fierce Pharma
Thu, 05/9/24 - 07:17 pm
gene therapy
Vertex Pharmaceuticals
Bluebird Bio
ASGCT24: Regeneron’s Gene Therapy Shows ‘Dramatic’ Hearing Improvement in Deaf Kids
BioSpace
Wed, 05/8/24 - 11:33 am
Regeneron
DB-OTO
genetic deafness
gene therapy
ASGCT
Sarepta Seeks Label Expansion, Bigger Market for DMD Gene Therapy
BioSpace
Wed, 05/8/24 - 11:13 am
Sarepta Therapeutics
DMD
Elevidys
gene therapy
Krystal Biotech touts topical gene therapy uptake, plots overseas launches
Fierce Pharma
Tue, 05/7/24 - 06:27 pm
Krystal Biotech
Vyjuvek
dystrophic epidermolysis bullosa
gene therapy
Verve moves forward with backup base editing therapy
BioPharma Dive
Tue, 05/7/24 - 11:29 am
Verve Therapeutics
clinical trials
gene therapy
heart disease
Vertex files FDA approval ask for next-gen cystic fibrosis candidate, resumes diabetes cell therapy trial
Fierce Biotech
Tue, 05/7/24 - 11:14 am
Vertex Pharmaceuticals
cystic fibrosis
Vanza Triple
FDA
gene therapy
First Patient Begins Newly Approved Sickle Cell Gene Therapy
NY Times, NY
Mon, 05/6/24 - 11:40 am
Bluebird Bio
gene therapy
sickle cell disease
patients
Lyfgenia
5 DMD Data Readouts to Watch in 2024
BioSpace
Mon, 05/6/24 - 11:24 am
DMD
clinical trials
Pfizer
gene therapy
fordadistrogene movaparvovec
Dyne Therapeutics
DYNE-251
Edgewise Therapeutics
EDG-5506
Capricor
CAP-1002
Avidity Biosciences
AOC 1044
FDA’s Accelerated Approval of Sarepta DMD Gene Therapy Comes Under Fire
BioSpace
Fri, 05/3/24 - 11:20 am
FDA
accelerated approvals
Sarepta Therapeutics
DMD
gene therapy
Pfizer hemophilia gene therapy arrives in US to uncertain future
BioPharma Dive
Fri, 04/26/24 - 11:15 am
Pfizer
gene therapy
FDA
hemophila B
Beqvez
Walgreens rolls out gene, cell therapy services
Beckers Hospital Review
Thu, 04/25/24 - 05:51 pm
Walgreens
cell therapy
gene therapy
Walgreens Specialty Pharmacy
AbbVie and Regenxbio’s ‘multibillion-dollar opportunity’ in vision loss gene therapy
Pharma Voice
Wed, 04/24/24 - 08:42 am
Regenxbio
AbbVie
gene therapy
ABBV-RGX-314
wet age-related macular degeneration
diabetic retinopathy
5 Cell and Gene Therapy Decisions to Watch in 2024
BioSpace
Mon, 04/22/24 - 11:38 am
cell therapy
gene therapy
Pfizer
Beqvez
hemophilia B
Abeona Therapeutics
pz-cel
recessive dystrophic epidermolysis bullosa
Rocket Pharmaceuticals
Kresladi
Leukocyte adhesion deficiency-1
Adaptimmune
afami-cel
advanced synovial sarcoma
Autolus Therapeutics
obe-cel
B cell acute lymphoblastic leukemia

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