hemophilia B

Pfizer doubles down with its 2nd FDA hemophilia approval in 6 months
Fierce Pharma
Sun, 10/13/24 - 11:29 am
Pfizer
FDA
hemophilia B
Beqvez
5 Cell and Gene Therapy Decisions to Watch in 2024
BioSpace
Mon, 04/22/24 - 11:38 am
cell therapy
gene therapy
Pfizer
Beqvez
hemophilia B
Abeona Therapeutics
pz-cel
recessive dystrophic epidermolysis bullosa
Rocket Pharmaceuticals
Kresladi
Leukocyte adhesion deficiency-1
Adaptimmune
afami-cel
advanced synovial sarcoma
Autolus Therapeutics
obe-cel
B cell acute lymphoblastic leukemia
Pfizer rings in New Year with hemophilia B gene therapy nod in Canada
Fierce Pharma
Wed, 01/3/24 - 05:10 pm
Pfizer
Canada
gene therapy
hemophilia B
Beqvez
First Gene Therapy for Hemophilia B, CSL's HEMGENIX®, Approved by the European Commission
BioSpace
Tue, 02/21/23 - 10:00 am
CSL
Europe
Hemgenix
gene therapy
hemophilia B
Pfizer says hemophilia B gene therapy controlled bleeding in key study
BioPharma Dive
Fri, 12/30/22 - 10:42 am
Pfizer
gene therapy
hemophilia B
fidanacogene elaparvovec
Despite Eye-Popping $3.5 Million Price Tag For Gene Therapy Hemgenix, Budget Impact For Most Payers Will Be Relatively Small
Forbes
Mon, 12/5/22 - 10:48 am
Hemgenix
gene therapy
hemophilia B
drug pricing
CSL
Freeline's One Dose Gene Therapy could Transform Hemophilia B Treatment
BioSpace
Sun, 07/24/22 - 07:56 pm
hemophilia
hemophilia B
clinical trials
Freeline Therapeutics
gene therapy
FLT180a
CSL-UniQure Hemophilia B Gene Therapy Scores Priority Review
BioSpace
Tue, 05/24/22 - 04:34 pm
CSL Behring
uniQure
hemophilia B
gene therapy
FDA
priority review
etranacogene dezaparvovec
Fresh data show UniQure's hemophilia gene therapy appears to hold up
BioPharma Dive
Fri, 12/10/21 - 12:01 am
uniQure
gene therapy
hemophilia
hemophilia B
Uniqure's Hemophilia B Gene Therapy Unlikely To Be Cause Of Liver Cancer Reported In One Patient
Benzinga
Mon, 03/29/21 - 10:36 am
uniQure
gene therapy
hemophilia B
etranacogene dezaparvovec
clinical trials
Gene therapy for hemophilia: So close, yet so far away
BioPharma Dive
Thu, 01/28/21 - 11:18 pm
hemophilia
hemophilia A
hemophilia B
gene therapy
Biomarin
uniQure
UniQure/CSL hit by FDA clinical hold for hem B gene therapy program after liver cancer find
Fierce Biotech
Mon, 12/21/20 - 11:09 am
uniQure
CSL
FDA
clinical trials
hemophilia B
gene therapy
etranacogene dezaparvovec
UniQure out-licenses hemophilia B gene therapy in deal valued up to ~$2.1B
Seeking Alpha
Wed, 06/24/20 - 11:29 pm
uniQure
CSL
hemophilia B
etranacogene dezaparvovec
Regeneron to expand development deal with Intellia Therapeutics
Marketwatch
Mon, 06/1/20 - 10:30 am
Regeneron
Intellia Therapeutics
hemophilia A
hemophilia B
CRISPR
drug development
Value-based pricing for gene therapy? Maybe not ready for hemophilia
Biopharma Dive
Thu, 12/12/19 - 10:52 am
Biomarin
hemophilia
hemophilia A
gene therapy
valoctocogene roxaparvovec
uniQure
hemophilia B
etranadez
UniQure stays a step ahead in hemophilia B
Biopharma Dive
Tue, 09/3/19 - 12:32 pm
uniQure
gene therapy
hemophilia B
clinical trials
AMT-061
This Gene Therapy Stock Could Soon Hit The Auction Block — Here's Why
Investors Business Daily
Sun, 02/10/19 - 01:48 pm
uniQure
M&A
hemophilia B
AMT-061
Pfizer
Spark Therapeutics
Uniqure turns the screw on Spark and Pfizer
EP Vantage
Fri, 02/8/19 - 11:37 am
uniQure
Spark Therapeutics
Pfizer
AMT-061
hemophilia B
UniQure’s hemophilia B gene therapy achieves 31% FIX activity
Fierce Biotech
Thu, 11/15/18 - 09:51 am
uniQure
hemophilia B
gene therapy
FIX-Padula
Pfizer's Hemophilia B Gene Therapy Candidate Enters Phase III
Zacks.com
Wed, 07/18/18 - 09:26 am
Pfizer
hemophilia B
gene therapy
fidanacogene elaparvovec

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