gene therapy

Pfizer injects $500M more into gene therapy manufacturing
Biopharma Dive
Wed, 08/21/19 - 11:44 pm
Pfizer
gene therapy
drug manufacturing
North Carolina
Sarepta now needs flawless progress for gene therapy
Biopharma Dive
Tue, 08/20/19 - 10:58 pm
Sarepta Therapeutics
FDA
Duchenne Muscular Dystrophy
Vyondys 53
gene therapy
SRP-9001
Gene therapies to test FDA's approach to regulating drugs after launch, experts say
Bizjournals
Fri, 08/16/19 - 10:04 am
gene therapy
FDA
Treating glioblastoma with a Ziopharm drug and IL-12 gene therapy
Fierce Biotech
Wed, 08/14/19 - 11:53 pm
Ziopharm Oncology
IL-12
gene therapy
glioblastoma
clinical trials
Patient in Sarepta gene therapy trial develops serious illness; shares plunge
Yahoo/Reuters
Thu, 08/8/19 - 11:34 pm
Sarepta Therapeutics
Duchenne Muscular Dystrophy
rhabdomyolysis
gene therapy
More M&A Activity Expected Around AAV-Based Gene Therapies, Analyst Says
BioSpace
Wed, 08/7/19 - 11:34 pm
gene therapy
M&A
Audentes Therapeutics
Regenxbio
Passage Bio
Novartis used manipulated data in winning Zolgensma approval, FDA says
Biopharma Dive
Wed, 08/7/19 - 10:57 am
Novartis
FDA
Zolgensma
data
spinal muscular atrophy
gene therapy
AveXis
BioMarin drops lower dose of its hemophilia gene therapy as it eyes submissions by year-end
Fierce Biotech
Fri, 08/2/19 - 10:37 am
Biomarin
hemophilia
gene therapy
valoctocogene roxaparvovec
valrox
hemophilia A
Amicus shares early look at Batten disease gene therapy
Fierce Biotech
Thu, 08/1/19 - 10:31 am
Amicus Therapeutics
Batten disease
gene therapy
AAV-CLN6
RegenxBio and Pfizer Partner on Gene Therapy for Friedreich's Ataxia
BioSpace
Wed, 07/31/19 - 11:50 pm
Regenxbio
Pfizer
gene therapy
Friedreich's Ataxia
Massachusetts General and ElevateBio Ink 10-Year Cell and Gene Therapy Deal
BioSpace
Thu, 07/25/19 - 10:40 pm
Massachusetts General Hospital
ElevateBio
cell therapy
gene therapy
R&D
Ultragenyx close to learning whether gene therapy gamble will pay off
Biopharma Dive
Fri, 07/19/19 - 12:51 pm
Ultragenyx
Dimension Therapeutics
gene therapy
DTX-301
DTX-401
Payers, patients coming on board for Novartis’ Zolgensma
BioCentury
Thu, 07/18/19 - 05:58 pm
Novartis
Zolgensma
SMA
gene therapy
payers
patients
Billions on the line: BioMarin bustles past enthused rival, planning to launch world’s first hemophilia A gene therapy
Endpoints
Mon, 07/8/19 - 08:13 pm
Biomarin
hemophilia A
gene therapy
FDA
Sangamo
Pfizer
Sangamo backs up early success for hemophilia gene therapy
Biopharma Dive
Sat, 07/6/19 - 01:36 pm
Sangamo
gene therapy
hemophilia A
SB-525
Pfizer
Spark Therapeutics
Biomarin
Novartis struggling to win payer coverage for $2.1M gene therapy Zolgensma: analysts
Fierce Pharma
Wed, 07/3/19 - 10:38 am
Novartis
Zolgensma
drug pricing
SMA
gene therapy
payers
Thermo Fisher to manufacture gene therapies being developed by Amicus
Fierce Pharma
Mon, 07/1/19 - 07:38 pm
Thermofisher
Amicus Therapeutics
gene therapy
CDMOs
3 Small-Cap Biotech Stocks That Soared Last Week
Motley Fool
Mon, 07/1/19 - 10:27 am
Dova Pharmaceuticals
Doptelet
Krystal Biotech
KB103
MeiraGTx
gene therapy
AAV-RPE65
Pfizer's DMD Gene Therapy Shows Severe Side Effects in Study
Yahoo/Zacks.com
Mon, 07/1/19 - 10:16 am
Pfizer
DMD
Duchenne Muscular Dystrophy
clinical trials
gene therapy
PF-06939926
Krystal looks to Phase III as stock soars on data for gene therapy
BioCentury
Tue, 06/25/19 - 09:15 am
Krystal Biotech
gene therapy
KB103

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