gene therapy

FDA, NIH, and 15 private organizations join forces to increase effective gene therapies for rare diseases
FDA
Wed, 10/27/21 - 11:49 pm
Bespoke Gene Therapy Consortium
NIH
FDA
gene therapy
ElevateBio cuts a deal for Life Edit, adding genome engineering tech to support gene therapy pipeline
Fierce Biotech
Wed, 10/27/21 - 11:05 am
Elevate Bio
Life Edit Therapeutics
gene therapy
genome editing
M&A
Novartis dumps Rett gene therapy caught up in Zolgensma scandal in cull of pipeline prospects
Fierce Biotech
Tue, 10/26/21 - 10:41 am
Novartis
Rett Syndrome
AVXS-201
Zolgensma
gene therapy
Bluebird, winding down in Europe, withdraws another rare disease gene therapy
BioPharma Dive
Thu, 10/21/21 - 11:17 pm
Bluebird Bio
gene therapy
Europe
Skysona
cerebral adrenoleukodystrophy
A California biotech steps into the viral vector space with new site build of $75M
Endpoints
Thu, 10/14/21 - 10:58 am
Avid Bioservices
cell therapy
gene therapy
California
CDMOs
Charles River Laboratories has been on an acquisition spree. But Tuesday, it offloaded two assets
Endpoints
Wed, 10/13/21 - 10:53 am
Charles River Laboratories
M&A
gene therapy
CDMOs
Poseida, Takeda partner to develop eight in vivo gene therapy programs
Pharmaceutical Business Review
Wed, 10/13/21 - 10:51 am
Takeda
Poseida Therapeutics
gene therapy
drug development
Sarepta outlines final push for Duchenne gene therapy
BioPharma Dive
Mon, 10/11/21 - 09:52 pm
Sarepta Therapeutics
gene therapy
Duchenne Muscular Dystrophy
clinical trials
Pfizer agrees $630m deal to harness Voyager’s gene therapy tech
Pharmaforum
Wed, 10/6/21 - 10:46 am
Pfizer
Voyager Therapeutics
gene therapy
Gemini axes CSO and 20% of staff to focus on late-phase plans
Fierce Biotech
Tue, 10/5/21 - 10:43 am
Gemini Therapeutics
layoffs
gene therapy
CSO
age-related macular degeneration
Takeda taps Selecta for $1.1B gene therapy research pact
Fierce Biotech
Mon, 10/4/21 - 10:43 am
Takeda
Selecta Biosciences
gene therapy
biobucks
Philadelphia Bursting at the Seams as Biopharma Hub Status Grows
BioSpace
Sun, 10/3/21 - 08:19 pm
Philadelphia
cell therapy
gene therapy
biotech hubs
For gene therapies, FDA drafts trial guidance, finalizes "sameness" for orphan exclusivity
RAPS.org
Thu, 09/30/21 - 11:06 pm
gene therapy
regulstory
FDA
cell therapy
Why AbbVie Just Made a $1.8 Billion Gene Therapy Deal
Motley Fool
Sat, 09/25/21 - 11:00 pm
AbbVie
Regenxbio
gene therapy
wet age-related macular degeneration
Kids suffer serious adverse reactions in AGTC gene therapy trial
Fierce Biotech
Fri, 09/24/21 - 12:04 pm
AGTC
gene therapy
pediatrics
clinical trials
rare disease
Ocular gene therapy biotech launches with $19M seed funding
Biopharma Reporter
Thu, 09/23/21 - 11:01 am
Opus Genetics
gene therapy
funding
ocular gene therapy
Novartis reshuffling doesn't portend a pullback from gene therapy, company says
Fierce Pharma
Wed, 09/22/21 - 11:56 am
Novartis
gene therapy
AveXis
Novartis acquires Arctos Medical to expand optogenetics portfolio
Biopharma Reporter
Tue, 09/21/21 - 10:50 am
Novartis
Arctos Medical
gene therapy
optogenetics
Zolgensma patent spat brews between Novartis and Regenxbio as top Novartis gene therapy exec departs
Endpoints
Mon, 09/20/21 - 11:15 am
Regenxbio
gene therapy
patents
Novartis
Zolgensma
SMA
Pfizer backs a small Swiss upstart's attempt to discover a non-viral gene therapy
Endpoints
Thu, 09/16/21 - 10:48 am
gene therapy
Switzerland
Pfizer
venture capital
funding
Anjarium Biosciences

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