Hunter Syndrome

RegenxBio touts positive data for rare disease drug RGX-121
Clinical Trials Arena
Wed, 09/4/24 - 11:20 am
Regenxbio
RGX-121
clinical trials
Hunter Syndrome
Denali Therapeutics Announces New Interim Data from Phase 1/2 Study of DNL310 (ETV:IDS) in MPS II (Hunter Syndrome) at SSIEM 2022
BioSpace
Wed, 08/31/22 - 10:19 pm
Denali Therapeutics
clinical trials
DNL310
Hunter Syndrome
RegenXBio gets FDA support for Hunter syndrome gene therapy's accelerated review filing—in 2024
Fierce Biotech
Wed, 08/3/22 - 10:58 am
Regenxbio
Hunter Syndrome
RGX-121
accelerated approval
FDA
Takeda Drops One Hunter Syndrome Therapeutic, Puts Faith in Another
BioSpace
Thu, 05/12/22 - 10:21 am
Takeda
earnings
TAK-609
Hunter Syndrome
Denali Therapeutics Sees Positive Data in Trial for Enzyme Replacement Therapy
Marketwatch
Mon, 07/26/21 - 09:42 am
Denali Therapeutics
DNL310
enzymes
Hunter Syndrome
clinical trials
Denali unveils first proof-of-concept for brain delivery tech in rare disease, with eyes on much bigger indications
Endpoints
Fri, 02/12/21 - 11:08 am
Denali Therapeutics
Hunter Syndrome
proof-of-concept
Sangamo falls on 16-week data from gene editing trial
BioCentury
Wed, 09/5/18 - 06:39 pm
Sangamo Therapeutics
Hunter Syndrome
SB-913
Shire hit by a setback as Hunter syndrome drug fails late-stage study
Endpoints
Tue, 12/19/17 - 12:04 pm
Shire
Hunter Syndrome
clinical trials
SHP609
Elaprase
Sangamo claims a major milestone in gene editing, treating first patient with its zinc finger nuclease tech
Endpoints
Wed, 11/15/17 - 11:06 am
Sangamo
gene editing
Hunter Syndrome
CRISPR
SB-913
Shire plans to spend about $225 million on collaboration over potential Hunter syndrome drug
Yahoo/AP
Wed, 07/23/14 - 09:14 am
Shire
Hunter Syndrome
ArmaGen
Shire pump bypasses hurdle to sneak enzyme drug into brain
Fierce Drug Delivery
Wed, 10/26/11 - 10:38 am
Shire
Hunter Syndrome
Elaprase