gene therapy

FDA explains plans to bolster cell and gene therapy approvals through wider messaging
RAPS.org
Thu, 05/19/22 - 09:01 pm
FDA
regulatory
cell therapy
gene therapy
With its lead gene therapy nearing the clinic, SwanBio leans heavily on Syncona to close $56M series B
Fierce Biotech
Wed, 05/18/22 - 10:25 am
Sycona
SwanBio Therapeutics
funding
gene therapy
Pfizer, Sarepta team with fellow DMD gene therapy makers to get to the bottom of adverse events
Fierce Biotech
Tue, 05/17/22 - 10:31 pm
Duchenne Muscular Dystrophy
gene therapy
Pfizer
Sarepta Therapeutics
Genethon
Solid Biosciences
Ultragenyx strikes deal with struggling Abeona for rare disease gene therapy
BioPharma Dive
Tue, 05/17/22 - 10:30 pm
Ultragenyx
Sanfillipo Syndrome
gene therapy
Abeona Therapeutics
Aiming to be biggest biotech in Boston, Vertex plots 500-person cell, gene therapy R&D center
Fierce Biotech
Tue, 05/17/22 - 10:54 am
Vertex Pharmaceuticals
Boston
cell therapy
gene therapy
Can FDA replicate Operation Warp Speed for rare diseases? Not yet, but Peter Marks has some ideas
Fierce Biotech
Wed, 05/11/22 - 10:29 am
FDA
Peter Marks
CBER
gene therapy
cell therapy
Operation Warp Speed
Rare Diseases
All Takeda wants for its billion-dollar gene therapy spending spree is functional cures
Fierce Biotech
Wed, 05/4/22 - 10:20 am
Takeda
gene therapy
rare disease
Another Pfizer gene therapy is free of FDA hold, but delay continues
Fierce Biotech
Tue, 05/3/22 - 10:53 pm
Pfizer
FDA
clinical trials
hemophilia A
gene therapy
giroctocogene fitelparvovec
Sangamo Therapeutics
WMIF panel: How cell and gene therapy can overcome limitations of CAR T
MedCity News
Tue, 05/3/22 - 10:35 am
CAR-T
cell therapy
gene therapy
solid tumors
World Medical Innovation Forum
Biogen takes another dip into Scribe gene therapy collab with another disease target
Fierce Biotech
Mon, 05/2/22 - 06:18 pm
Biogen
Scribe Therapeutics
gene therapy
CRISPR
FDA clears Pfizer to restart Duchenne gene therapy trial, with new safeguards
BioPharma Dive
Thu, 04/28/22 - 10:56 am
Pfizer
gene therapy
Duchenne Muscular Dystrophy
clinical trial
FDA
Sio Gene could be a canary in the coalmine for gene therapy
EP Vantage
Thu, 04/28/22 - 10:42 am
Sio Gene
Axovant
gene therapy
Zolgensma for dementia? AviadoBio gains orphan tag for one-dose gene therapy
Fierce Biotech
Wed, 04/27/22 - 10:51 pm
AviadoBio
demential
Zolgensma
AVB-101
gene therapy
Undeterred by gene therapy’s struggles, a startup launches into a downturn
BioPharma Dive
Tue, 04/26/22 - 10:29 am
gene therapy
funding
startups
Apertura Gene Therapies
Astellas, Tmunity, Underscore Rocky Terrain of CAR-T and Gene Therapies
BioSpace
Mon, 04/25/22 - 10:38 pm
Astellas
Tmunity
CAR-T
gene therapy
myotubular myopathy
Astellas takes $170m charge as it drops DMD gene therapies
Pharmaforum
Fri, 04/22/22 - 10:48 am
Astellas
gene therapy
Duchenne Muscular Dystrophy
earnings
Takeda/Evozyne Partnership Headlines Hot Week for Gene Therapy Deals
BioSpace
Wed, 04/6/22 - 07:37 pm
Takeda
Evozyne
gene therapy
Rare Diseases
Hunting for next big eye disease drug, Regeneron gets deeper into gene therapies with ViGeneron pact
Fierce Biotech
Wed, 04/6/22 - 12:18 pm
Regeneron
gene therapy
ViGeneron
retinal disease
FDA releases draft guidance for cell and gene therapies
Biopharma Reporter
Wed, 04/6/22 - 11:35 am
FDA
regulatory
cell therapy
gene therapy
CAR-T
Big Pharma partnerships, record $22.7B investment raise profile of regenerative medicine in 2021
Fierce Biotech
Tue, 04/5/22 - 11:41 pm
regenerative medicine
gene editing
gene therapy
Big Pharma
Intellia Therapeutics

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