Rett Syndrome

Neurogene drops high-dose arm in Rett study after death
Pharmaphorum
Fri, 11/22/24 - 11:09 am
Neurogene
clinical trials
Rett Syndrome
patient death
gene therapy
NGN-401
Neurogene falls again on Rett gene therapy side effects
Pharmaphorum
Mon, 11/18/24 - 11:11 am
Neurogene
Rett Syndrome
clinical trials
gene therapy
Neurogene’s stock sinks after adverse event with Rett syndrome gene therapy
Clinical Trials Arena
Tue, 11/12/24 - 10:59 am
Neurogene
Rett Syndrome
gene therapy
clinical trials
Neurogene secures $200M ahead of anticipated study readout
BioPharma Dive
Mon, 11/4/24 - 06:55 pm
Neurogene
funding
Rett Syndrome
NGN-401
Acadia wins first FDA approval for Rett syndrome drug
Endpoints
Mon, 03/13/23 - 10:04 am
Acadia Pharmaceuticals
FDA
Daybue
Rett Syndrome
5 FDA decisions to watch in the first quarter
BioPharma Dive
Mon, 01/9/23 - 10:27 am
FDA
Eli Lilly
donanemab
Alzheimer's disease
Menareni
Elacestrant
breast cancer
Biomarin
Roctavian
hemophilia A
Acadia Pharmaceuticals
trofinetide
Rett Syndrome
Gilead Sciences
Trodelvy
Astellas Pays $50M for Access to Taysha's Rett, GAN Programs
BioSpace
Wed, 10/26/22 - 10:29 am
Taysha Gene Therapies
Astellas
gene therapy
Rett Syndrome
GAN
Acadia closer to bringing first Rett syndrome drug to market
Pharmaforum
Wed, 12/8/21 - 10:33 am
Acadia Pharma
trofinetide
clinical trials
Rett Syndrome
Novartis dumps Rett gene therapy caught up in Zolgensma scandal in cull of pipeline prospects
Fierce Biotech
Tue, 10/26/21 - 10:41 am
Novartis
Rett Syndrome
AVXS-201
Zolgensma
gene therapy
Newron's Merck KGaA-in licensed compound fails Rett Syndrome study, shares wilt
Endpoints
Mon, 05/4/20 - 10:32 am
Newron Pharma
Merck KGaA
Rett Syndrome
sarizotan
clinical trials
Upcoming events – Obseva's first fibroid foray and Newron's test in Retts
EP Vantage
Fri, 09/6/19 - 10:12 am
clinical trials
ObsEva
uterine fibroids
linzagolix
Newron Pharma
Rett Syndrome
Acadia to Move Experimental Pediatric Rett Syndrome Drug to Phase 3
Xconomy
Wed, 03/27/19 - 11:41 pm
Acadia Pharmaceuticals
pediatrics
Rett Syndrome
clinical trials
trofinetide