Rocket begins patient dosing in phase 1 trial of RP-A501 in Danon disease

Rocket begins patient dosing in phase 1 trial of RP-A501 in Danon disease

Source: 
Pharmaceutical Business Review
snippet: 

Rocket Pharmaceuticals, Inc. (NASDAQ: RCKT) (“Rocket”), a leading U.S.-based multi-platform clinical-stage gene therapy company, today announces that patient dosing has commenced in the open-label, Phase 1 clinical trial of RP-A501, the Company’s adeno-associated viral vector (AAV)-based gene therapy for the treatment of Danon disease.