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RP-A501
Rocket boosted as FDA alignment on pivotal gene therapy trial design sends stock skyward
Rocket boosted as FDA alignment on pivotal gene therapy trial design sends stock skyward
Fierce Biotech
Rocket Pharmaceuticals
gene therapy
FDA
clinical trials
RP-A501
Danon disease
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New pediatric data shoot Rocket's gene therapy toward phase 2, leaving behind FDA concerns
New pediatric data shoot Rocket's gene therapy toward phase 2, leaving behind FDA concerns
Fierce Biotech
Rocket Pharmaceuticals
gene therapy
clinical trials
RP-A501
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Rocket begins patient dosing in phase 1 trial of RP-A501 in Danon disease
Rocket begins patient dosing in phase 1 trial of RP-A501 in Danon disease
Pharmaceutical Business Review
Rocket Pharmaceuticals
gene therapy
Danon disease
RP-A501
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Rocket Pharmaceuticals Releases Preclinical Data for First Investigational Gene Therapy Program for Rare Heart Disorder
Rocket Pharmaceuticals Releases Preclinical Data for First Investigational Gene Therapy Program for Rare Heart Disorder
CP Wire
Rocket Pharmaceuticals
RP-A501
Danon disease
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Rocket Pharmaceuticals Releases Preclinical Data for First Investigational Gene Therapy Program for Rare Heart Disorder
Rocket Pharmaceuticals
RP-A501
Danon disease
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