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gene therapies

Medicaid, with planned payment pilot, girds for influx of pricey gene therapies

BioPharma Dive

Tue, 02/21/23 - 04:37 pm

sickle cell disease

Vertex Pharmaceuticals

CRISPR Therapeutics

ASH 2022 – Orchard gets a Sanfilippo boost

EP Vantage

Tue, 12/13/22 - 10:24 am

Orchard Therapeutics

Sanfillipo Syndrome

Locanabio Raises $100 Million to Advance RNA-Targeted Gene Therapies

BioSpace

Mon, 12/14/20 - 11:07 pm

Generation Bio grabs a $110M round to ramp up work on next-gen gene therapies

Fierce Biotech

Fri, 01/10/20 - 10:40 am

phenylketonuria

Sarepta pays StrideBio $48M for preclinical gene therapies

Fierce Biotech

Fri, 11/15/19 - 11:09 am

Sarepta Therapeutics

Ophthotech (now Iveric) hits eye drug goals as shares jump for tiny biotech

Fierce Biotech

Mon, 10/28/19 - 10:36 am

dry age-related macular degeneration

AskBio Reels In $235M to Advance Gene Therapy Clinical Trials

Xconomy

Thu, 04/11/19 - 12:31 pm

Asklepios BioPharmaceutical

Rare genetic disease company Homology raises $125M follow-on

BioCentury

Wed, 04/10/19 - 11:42 pm

Novartis' AveXis buys AstraZeneca site in Colorado as it anticipates gene therapy launch

Fierce Pharma

Tue, 04/2/19 - 11:54 am

drug manufacturing

As promised, Novartis eyes new method for funding ultrapricey next-gen drugs: FT

Fierce Pharma

Wed, 12/19/18 - 12:37 am

Express Scripts staking out million-dollar gene therapies

Reuters

Wed, 08/15/18 - 10:32 pm

Express Scripts

Spark Therapeutics

FDA plans to speed path to approval for some gene therapies, starting with hemophilia

Stat

Tue, 05/22/18 - 06:38 pm

Here Come More Gene Therapies -- And More Pricing Debates

Forbes

Wed, 10/11/17 - 10:03 am

Spark Therapeutics

Regenxbio to buy battered Dimension for gene therapies

Fierce Biotech

Mon, 08/28/17 - 09:38 am

Dimension Therapeutics