Sanfillipo Syndrome

ASH 2022 – Orchard gets a Sanfilippo boost
EP Vantage
Tue, 12/13/22 - 10:24 am
ASH 2022
Orchard Therapeutics
Sanfillipo Syndrome
gene therapies
OTL-201
Lysogene's lead gene therapy flunks phase 2/3 trial almost a year after Sarepta walked out
Fierce Biotech
Sun, 11/20/22 - 12:54 pm
Lysogene
gene therapy
clinical trials
LYS-SAF302
Sanfillipo Syndrome
Ultragenyx strikes deal with struggling Abeona for rare disease gene therapy
BioPharma Dive
Tue, 05/17/22 - 10:30 pm
Ultragenyx
Sanfillipo Syndrome
gene therapy
Abeona Therapeutics
Seelos Therapeutics Files Paperwork for $14 Million Offering
CP WIre
Wed, 01/22/20 - 11:14 am
Seelos Therapeutics
Sanfillipo Syndrome
PTSD
suicidal ideation
Seelos Therapeutics Files Paperwork for $14 Million Offering
Wed, 01/22/20 - 11:12 am
Seelos Therapeutics
Sanfillipo Syndrome
PTSD
suicidal ideation