Duchenne Muscular Dystrophy

Another Duchenne clinical hold gets lifted, this time at Dyne Therapeutics
Endpoints
Tue, 07/5/22 - 10:45 am
Duchenne Muscular Dystrophy
clinical trials
Dyne Therapeutics
DYNE-251
As muscular dystrophy drug meets key goal, Italfarmaco plans march forward to regulators
MedCity News
Mon, 06/27/22 - 10:15 am
Duchenne Muscular Dystrophy
Italy
Ifalfarmco
givinostat
FDA suspends US testing of Sarepta Duchenne drug over safety concerns
BioPharma Dive
Thu, 06/23/22 - 08:04 pm
FDA
Sarepta Therapeutics
Duchenne Muscular Dystrophy
SRP-5051
PTC Ready to Take Another Shot at FDA Approval of DMD Drug
BioSpace
Tue, 06/21/22 - 10:58 am
PTC Therapeutics
Translarna
FDA
Duchenne Muscular Dystrophy
Pfizer, Sarepta team with fellow DMD gene therapy makers to get to the bottom of adverse events
Fierce Biotech
Tue, 05/17/22 - 10:31 pm
Duchenne Muscular Dystrophy
gene therapy
Pfizer
Sarepta Therapeutics
Genethon
Solid Biosciences
With Sarepta in its sights, PepGen prices IPO to fund DMD trials
Fierce Biotech
Fri, 05/6/22 - 10:55 am
PepGen
IPOs
Sarepta Therapeutics
Duchenne Muscular Dystrophy
FDA clears Pfizer to restart Duchenne gene therapy trial, with new safeguards
BioPharma Dive
Thu, 04/28/22 - 10:56 am
Pfizer
gene therapy
Duchenne Muscular Dystrophy
clinical trial
FDA
Roche delays DMD drug deadline, decides to rejig MS trials because of Ukraine war
Fierce Biotech
Tue, 04/26/22 - 10:33 am
Roche
Ocrevus
clinical trials
Duchenne Muscular Dystrophy
Astellas takes $170m charge as it drops DMD gene therapies
Pharmaforum
Fri, 04/22/22 - 10:48 am
Astellas
gene therapy
Duchenne Muscular Dystrophy
earnings
Pfizer aims to restart late-stage trial of Duchenne gene therapy following safety setback
BioPharma Dive
Thu, 02/10/22 - 08:04 pm
Pfizer
gene therapy
Duchenne Muscular Dystrophy
clinical trials
Sarepta says early filing for DMD gene therapy may be back on
Pharmaforum
Wed, 01/12/22 - 10:53 am
Sarepta Therapeutics
Duchenne Muscular Dystrophy
SRP-9001
Sarepta DMD Treatment Improves Motor Skills in Study Presented at JPM
BioSpace
Tue, 01/11/22 - 11:41 am
Sarepta Therapeutics
delandistrogene moxeparvovec
Duchenne Muscular Dystrophy
JPMHC 2022
Sarepta, with new Duchenne results, to broach 'possibility' of speedy gene therapy approval
BioPharma Dive
Mon, 01/10/22 - 11:39 pm
Sarepta Therapeutics
Duchenne Muscular Dystrophy
gene therapy
Pfizer reports patient death in early-stage Duchenne gene therapy trial, halts enrollment
Fierce Biotech
Tue, 12/21/21 - 10:28 am
Pfizer
clinical trials
Duchenne Muscular Dystrophy
gene therapy
patient deaths
PF-06939926
Buoyed by new data, Santhera preps filing for DMD drug vamorolone
Pharmaforum
Tue, 11/23/21 - 09:43 am
Santhera
DMD
Duchenne Muscular Dystrophy
idebenone
vamorolone
FDA
Pfizer tears up gene therapy timelines, revealing a series of phase 3 delays that end vision of a banner 2022
Fierce Biotech
Wed, 11/3/21 - 10:43 am
Pfizer
gene therapy
hemophilia
Duchenne Muscular Dystrophy
Sangamo Therapeutics
Sarepta outlines final push for Duchenne gene therapy
BioPharma Dive
Mon, 10/11/21 - 09:52 pm
Sarepta Therapeutics
gene therapy
Duchenne Muscular Dystrophy
clinical trials
Capricor's DMD clinical trial meets primary endpoints
Endpoints
Fri, 09/24/21 - 11:52 am
Capricor
clinical trials
Duchenne Muscular Dystrophy
CAP-1002
8 key clinical trials to watch for the rest of 2021
BioPharma Dive
Mon, 06/21/21 - 11:11 am
clinical trials
Merck
Ridgeback Biotherapeutics
COVID-19
Intellia Therapeutics
transthyretin amyloidosis
Arcus Biosciences
Gilead Sciences
lung cancer
Sanofi
GSK
vaccines
uniQure
Huntington's disease
Mirati Therapeutics
gene editing
Seres Therapeutics
ulcerative colitis
Sarepta Therapeutics
Duchenne Muscular Dystrophy
Months after axing a Duchenne program and laying off dozens, Santhera claims a win there with a different program
Endpoints
Tue, 06/1/21 - 11:43 am
Santhera Pharmaceuticals
Duchenne Muscular Dystrophy
vamorolone
clinical trials

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