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gene therapy

Freshly IPO’d Tocagen tweaks brain cancer gene therapy test

Fierce Biotech

Sat, 10/28/17 - 11:14 pm

GSK picks up NICE recommendation for Strimvelis, a €594,000 gene therapy

Fierce Pharma

Mon, 10/23/17 - 09:55 pm

We may soon have our first $1 million drug. Who will pay for it? And how?

Stat

Sat, 10/14/17 - 11:04 am

Spark Therapeutics

Spark’s Gene Therapy to Restore Vision Wins Unanimous FDA Panel Vote

Xconomy

Thu, 10/12/17 - 10:22 pm

Spark Therapeutics

advisory panels

FDA To Advisors: What If One-Time Gene Therapy Needs Extra Doses?

Xconomy

Tue, 10/10/17 - 11:26 pm

Spark Therapeutics

Spark Therapeutics faces a grilling as FDA ponders a pioneering OK for gene therapy

Endpoints

Tue, 10/10/17 - 09:38 am

Spark Therapeutics

retinal dystrophies

Bluebird’s gene therapy halts progression of ‘devastating’ disease cALD

Fierce Biotech

Fri, 10/6/17 - 09:48 am

AveXis gets FDA nod for pivotal gene therapy trial

Biopharma Dive

Mon, 10/2/17 - 11:05 am

Big Pharma Doesn't Want Health Outcomes To Sway Pricing -- At Least Not Yet

Forbes

Fri, 09/29/17 - 11:53 am

Express Scripts' Miller Backs New Pricing Models for CAR-T

BioCentury

Fri, 09/22/17 - 09:13 am

Express Scripts

On CAR-T’s Edge, Seattle Researchers Plot to Bypass Novartis Therapy

Xconomy

Tue, 09/19/17 - 08:43 am

Seattle Children's

pediatric cancer

Bidding war erupts over Dimension’s gene therapy pipeline as Ultragenyx counters Regenxbio deal

Endpoints

Mon, 09/18/17 - 09:26 am

Dimension Therapeutics

Profit finally in sight for gene therapy specialist Oxford Bio

Yahoo/Reuters

Wed, 08/23/17 - 10:07 pm

Oxford BioMedica

Pfizer commits $100M for a gene therapies plant in North Carolina

Fierce Pharma

Thu, 08/10/17 - 10:45 am

drug manufacturing

Is This Why bluebird bio Dipped 10.5% in July?

Motley Fool

Wed, 08/9/17 - 09:35 am

bluebird bio Pauses During 2017 Data Blitz

Motley Fool

Mon, 08/7/17 - 05:59 pm

Spark offers a glimpse of efficacy in first two hemophilia A gene therapy patients

Endpoints

Wed, 08/2/17 - 09:39 am

Spark Therapeutics

FDA embraces the first US application for a gene therapy, offering an accelerated test case

Endpoints

Mon, 07/17/17 - 09:59 am

Spark Therapeutics

RPE65-mediated inherited retinal disease

BioMarin, Spark, raising the stakes for hemophilia

BioPharma Dive

Wed, 07/12/17 - 02:48 pm

Spark Therapeutics

FDA panel to focus on safety of Novartis gene therapy drug

Yahoo/Reuters

Mon, 07/10/17 - 09:32 am

advisory panels

acute lymphoblastic leukemia

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