gene therapy

Boehringer Ingelheim lands option on cystic fibrosis gene therapy
Fierce Biotech
Mon, 08/6/18 - 09:58 am
Boehringer Ingelheim
cystic fibrosis
Oxford BioMedica
gene therapy
Bluebird’s first gene therapy gets European fast track
PM Live
Sat, 07/28/18 - 12:26 pm
Bluebird Bio
gene therapy
EMA
LentiGlobin
FDA slaps a hold on Sarepta’s Duchenne MD study in the wake of stellar early results
Endpoints
Thu, 07/26/18 - 11:53 am
Sarepta Therapeutics
Duchenne Muscular Dystrophy
FDA
clinical hold
gene therapy
Nabbing late-stage drug, PTC acquires gene therapy startup Agilis for $200M in cash/stock
Endpoints
Thu, 07/19/18 - 11:23 pm
PTC Therapeutics
gene therapy
M&A
Agilis
Pfizer's Hemophilia B Gene Therapy Candidate Enters Phase III
Zacks.com
Wed, 07/18/18 - 09:26 am
Pfizer
hemophilia B
gene therapy
fidanacogene elaparvovec
FDA Releases Six New Draft Guidances on Gene Therapy
CP Wire
Thu, 07/12/18 - 10:03 am
FDA
Scott Gottlieb
gene therapy
FDA Releases Six New Draft Guidances on Gene Therapy
Thu, 07/12/18 - 10:03 am
FDA
gene therapy
Scott Gottlieb
Focused on rebuilding the pipeline, Axovant’s new crew assembles another preclinical gene therapy deal
Endpoints
Mon, 07/9/18 - 10:55 am
Axovant Sciences
AXO-Lenti-PD
gene therapy
RNAi
Benitec
Why bluebird bio's Shares Have Tumbled 11.9% in 2018 So Far
Motley Fool
Mon, 07/9/18 - 10:48 am
Bluebird Bio
gene therapy
beta thalassemia
LentiGlobin
3 Best Gene Therapy Stocks of 2018 (So Far)
Motley Fool
Thu, 07/5/18 - 11:04 am
gene therapy
FDA
Sarepta Therapeutics
Solid Biosciences
Regnxbio
The Human Genome Project: At the Root of a Healthcare Revolution
Yahoo/Motley Fool
Sat, 06/30/18 - 04:07 pm
Human Genome Project
DNA sequencing
gene therapy
drug development
Demand For Gene Therapies To Prompt Surge In Pharma M&A
Forbes
Tue, 06/19/18 - 10:11 pm
gene therapy
M&A
Bluebird Bio
Sangamo Therapeutics
Bluebird Bio Announces More Good News for LentiGlobin Gene Therapy – Exciting Results in Sickle Cell Disease
CP Wire
Fri, 06/15/18 - 10:02 am
Bluebird Bio
sickle cell disease
LentiGlobin
gene therapy
Bluebird Bio Presents Promising Results for Gene Therapy in Rare Blood Disorder
CP Wire
Fri, 06/15/18 - 10:01 am
Bluebird Bio
gene therapy
LentiGlobin
beta thalassemia
sickle cell disease
Novartis' brand-new gene therapy player AveXis will build $55M plant, hire 200
Fierce Pharma
Wed, 05/23/18 - 03:03 pm
Novartis
AveXis
gene therapy
drug manufacturing
Is biopharma’s first $1.5M therapy now in Phase III?
Endpoints
Mon, 05/7/18 - 11:12 am
drug pricing
gene therapy
Luxturna
Spark Therapeutics
First Patient Dosed in Avexis' Phase 3 Trial of AVXS-101 in Pre-Symptomatic Spinal Muscular Atrophy
CP Wire
Wed, 04/25/18 - 10:29 pm
AveXis
Novartis
M&A
clinical trials
AVXS-101
gene therapy
spinal muscular atrophy
Bluebird’s gene therapy for beta-thalassemia falls short of a cure, but still wows in 22 patients
Endpoints
Wed, 04/18/18 - 11:04 pm
Bluebird Bio
beta-thalassemia
gene therapy
[video]Did Novartis Overpay for AveXis?
Motley Fool
Mon, 04/16/18 - 11:34 pm
Novartis
AveXis
gene therapy
M&A
GSK slims portfolio with sale of rare disease gene therapy drugs
Yahoo/Reuters
Thu, 04/12/18 - 12:02 pm
GSK
Orchard Therapeutics
gene therapy
Rare Diseases

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