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» muscular dystrophy
muscular dystrophy
Sarepta adds another gene therapy to its ever-expanding pipeline
Sarepta adds another gene therapy to its ever-expanding pipeline
Biopharma Dive
Sarepta Therapeutics
muscular dystrophy
Limb Girdle Muscular Dystrophy
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Sarepta, in shadow of FDA setback, marks gene therapy progress
Sarepta, in shadow of FDA setback, marks gene therapy progress
BioPharma Dive
Sarepta Therapeutics
SRP-9003
limb-girdle muscular dystrophy
muscular dystrophy
gene therapy
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Suvodirsen For Duchenne Muscular Dystrophy Selected for FDA Complex Innovative Trial Designs Pilot Program
Suvodirsen For Duchenne Muscular Dystrophy Selected for FDA Complex Innovative Trial Designs Pilot Program
CP Wire
suvodirsen
Wave Life Sciences
Duchenne Muscular Dystrophy
muscular dystrophy
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Suvodirsen For Duchenne Muscular Dystrophy Selected for FDA Complex Innovative Trial Designs Pilot Program
suvodirsen
Wave Life Sciences
Duchenne Muscular Dystrophy
muscular dystrophy
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Orphan Drug Designation Granted to Investigational Gene Therapy for Rare Form of Muscular Dystrophy
Orphan Drug Designation Granted to Investigational Gene Therapy for Rare Form of Muscular Dystrophy
CP Wire
Limb Girdle Muscular Dystrophy
muscular dystrophy
FDA
Myonexus
NYO-102
gene therapy
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Myonexus Therapeutics Starts Trial of First-Ever Gene Therapy for Rare Type of Muscular Dystrophy
Myonexus Therapeutics Starts Trial of First-Ever Gene Therapy for Rare Type of Muscular Dystrophy
CP Wire
Myonexus
Sarepta Therapeutics
muscular dystrophy
gene therapy
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Myonexus Therapeutics Starts Trial of First-Ever Gene Therapy for Rare Type of Muscular Dystrophy
Myonexus
Sarepta Therapeutics
muscular dystrophy
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The Good, the Bad, and the Ugly of a Competitor's Failure
The Good, the Bad, and the Ugly of a Competitor's Failure
Motley Fool
GSK
Prosensa
Duchenne Muscular Dystrophy
muscular dystrophy
eteplirsen
Sarepta Therapeutics
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Potential Paradigm Shifting Technology from a Small Biotech
Potential Paradigm Shifting Technology from a Small Biotech
Motley Fool
Sarepta Therapeutics
eteplirsen
muscular dystrophy
Duchenne Muscular Dystrophy
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Buy, Sell, or Hold: Sarepta Therapeutics
Buy, Sell, or Hold: Sarepta Therapeutics
Motley Fool
Sarepta Therapeutics
Duchenne Muscular Dystrophy
muscular dystrophy
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Will Sarepta Receive Accelerated Approval?
Will Sarepta Receive Accelerated Approval?
Motley Fool
Sarepta
eteplirsen
muscular dystrophy
Duchenne Muscular Dystrophy
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Sarepta Therapeutics: Tomorrow's Monster Stock
Sarepta Therapeutics: Tomorrow's Monster Stock
Motley Fool
Sarepta Therapeutics
eterplirsen
Duchenne Muscular Dystrophy
muscular dystrophy
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Step Back From That Overnight Triple, Sir
Step Back From That Overnight Triple, Sir
Motley Fool
Sarepta Therapeutics
Duchenne Muscular Dystrophy
muscular dystrophy
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This Drug Could Be a Game-Changer for Sarepta (and a Savior for Thousands)
This Drug Could Be a Game-Changer for Sarepta (and a Savior for Thousands)
Motley Fool
Sarepta Therapeutics
muscular dystrophy
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Biogen Idec Inc. and Isis Pharmaceuticals Inc. to Work Together in a Project
Biogen Idec Inc. and Isis Pharmaceuticals Inc. to Work Together in a Project
French Tribune, France
Biogen Idec
Isis Pharmaceuticals
muscular dystrophy
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Biogen Idec and Isis Pharmaceuticals Announce Global Collaboration for Antisense Program Targeting Myotonic Dystrophy
Biogen Idec and Isis Pharmaceuticals Announce Global Collaboration for Antisense Program Targeting Myotonic Dystrophy
Yahoo
Isis Pharmaceuticals
Biogen Idec
antisense
muscular dystrophy
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Drug for rare disease may lift AVI BioPharma shares: Barron's
Drug for rare disease may lift AVI BioPharma shares: Barron's
Yahoo/Reuters
AVI BioPharma
eteplirsen
muscular dystrophy
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Insmed shares plummet on Iplex study results
Insmed shares plummet on Iplex study results
Yahoo/AP
Insmed
drug trials
IPLEX
muscular dystrophy
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