Myonexus Therapeutics Starts Trial of First-Ever Gene Therapy for Rare Type of Muscular Dystrophy

Myonexus Therapeutics Starts Trial of First-Ever Gene Therapy for Rare Type of Muscular Dystrophy

Source: 
CP Wire
snippet: 
  • In a mouse model, greater than 95% of muscle cells produced the beta-sarcoglycan protein after a single application
  • Myonexus and Sarepta are advancing four additional candidates
  • Sarepta has the option to purchase Myonexus at any point during their collaboration