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» Vertex Pharmaceutical
Vertex Pharmaceutical
Two Sickle Cell Disease Gene Therapies May Soon Be Approved By FDA
Forbes
Thu, 11/2/23 - 05:07 pm
sickle cell disease
gene therapy
lovo-cel
exa-cel
Vertex Pharmaceutical
CRISPR Therapeutics
Bluebird Bio
10 clinical trials to watch in the second half of 2023
BioPharma Dive
Mon, 08/7/23 - 10:32 am
clinical trials
Sarepta Therapeutics
DMD
Elevidys
Bridge Bio
ATTR-CM
acoramidis
Sanofi
Merck KGaA
MS
tolebrutinib
Pfizer
obesity
danuglipron
Novo Nordisk
Ozempic
Verve Therapeutics
heterozygous familial hypercholesterolemia
Roche
lung cancer
tiragolumab
Vertex Pharmaceutical
VS-548
pain
JNJ
Bristol Myers Squibb