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» orphan drugs
orphan drugs
NPS Pharma Drifts Higher On Potential Orphan Drug Approval
Seeking Alpha
Tue, 12/4/12 - 01:33 pm
NPS Pharmaceuticals
orphan drugs
short bowel syndrome
Gattex
Orphan Drug Status Potentially Huge For DARA Bio
Seeking Alpha
Thu, 11/29/12 - 11:58 am
DARA Biosciences
orphan drugs
KRN5500
chronic chemotherapy-induced peripheral neuropathy
Alnylam Pharmaceuticals, BioMarin Pharmaceutical Inc., and Cytonet Set to Speak on Conducting Effective Orphan Drug Research
CP Wire
Fri, 11/16/12 - 10:27 am
Alnylam
Cytonet
Biomarin
orphan drugs
Cleveland BioLabs hepatocellular carcinoma drug granted orphan status by FDA
Yahoo/Fly the on Wall
Mon, 10/1/12 - 09:47 pm
orphan drugs
hepatocellular carcinoma
Cleveland BioLabs
Quinacrine
Twin Orphan Drug News
Motley Fool
Sat, 09/29/12 - 11:50 am
Biomarin
orphan drugs
Peg-Pal
phenylketonuria
Kuvan
XOMA Receives Orphan Drug Designation From U.S. Food & Drug Administration for Gevokizumab
Yahoo
Thu, 08/23/12 - 09:58 am
Xoma
FDA
orphan drugs
gevokizumab
uveitis
Clovis Oncology ovarian cancer treatment receives orphan status
Yahoo/Fly on the Wall
Fri, 08/3/12 - 11:26 am
ovarian cancer
orphan drugs
Clovis Oncology
Senesco’s Lead Therapeutic Candidate, SNS01-T, Granted Orphan Drug Status from FDA for Treatment of Mantle Cell Lymphoma and Diffuse Large B-Cell Lymphoma
Yahoo
Mon, 07/30/12 - 11:06 am
Senesco
SNS01-T
orphan drugs
mantle cell lymphoma
diffuse large B-cell lymphoma
Athersys receives orphan drug designation for MultiStem
The Fly on the Wall
Tue, 07/10/12 - 12:11 pm
orphan drugs
MultiStem
Athersys
Alnylam gets orphan status for drug candidate
Yahoo/AP
Tue, 06/19/12 - 04:43 pm
Alnylam
orphan drugs
ALN-TTR02
NPS Pharmaceuticals: The Next Orphan-Drug Powerhouse?
Seeking Alpha
Tue, 04/24/12 - 10:33 am
orphan drugs
NPS Pharmaceuticals
Gattex
Natpara
Rare-disease drugs won't help out-of-work pharma reps
Fierce Pharma
Mon, 04/2/12 - 12:24 pm
drug reps
layoffs
orphan drugs
QLT Inc. receives Orphan Drug Designation for Visudyne
The Fly on the Wall
Mon, 03/19/12 - 10:24 am
orphan drugs
Visudyne
QLT
central serous chorioretinopathy
Celator Pharmaceuticals Receives EMA Orphan Drug Status for CPX-351 in Acute Myeloid Leukemia
Fierce Biotech
Sat, 01/28/12 - 12:46 pm
Celator
CPX-351
leukemia
acute myeloid leukemia
orphan drugs
Emergent BioSolutions potential leukemia treatment receives 'orphan drug' status from FDA
Yahoo/AP
Thu, 12/1/11 - 12:56 pm
FDA
orphan drugs
Emergent BioSolutions
leukemia
TRU-016
non-Hodgkin's lymphoma
chronic lymphocytic leukemia
Getting More Drugs Approved for Rare Diseases
WSJ Online
Wed, 07/6/11 - 10:18 am
drug approvals
FDA
orphan drugs
FDA grants "orphan drug" status to CytRx's experimental cancer drug
Yahoo/AP
Tue, 07/5/11 - 04:44 pm
orphan drugs
FDA
CytRx
INNO-206
cancer
Push to spur more drugs for deadly rare diseases
Yahoo/AP
Tue, 04/26/11 - 06:15 am
orphan drugs
Nektar ovarian cancer drug gets FDA orphan status
Bizjournals.com
Thu, 04/21/11 - 06:53 pm
orphan drugs
ovarian cancer
FDA
Nektar
NKTR-102
Sanofi plans autonomy for part of Genzyme business
Yahoo/AP
Thu, 03/3/11 - 07:24 am
M&A
Genzyme
Sanofi
orphan drugs
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