orphan drugs

Orphan drug market to reach $270B by 2028, led by J&J, Vertex and Roche
Fierce Pharma
Wed, 04/24/24 - 08:50 am
orphan drugs
Evaluate Pharma
JNJ
Vertex Pharmaceuticals
Roche
Candel wins FDA orphan drug designation for pancreatic cancer drug
Clinical Trials Arena
Sun, 04/14/24 - 01:23 pm
FDA
Candel Therapeutics
CAN-2409
pancreatic cancer
orphan drugs
NeoImmuneTech receives orphan drug status for NT-I7 to treat ARS
Pharmaceutical Business Review
Tue, 11/21/23 - 11:59 am
NeoImmune Tech
FDA
NT-I7
acute radiation syndrome
orphan drugs
FDA grants orphan drug designation to Faron’s bexmarilimab
Pharmaceutical Business Review
Wed, 08/30/23 - 10:07 am
Faron Pharmaceuticals
FDA
orphan drugs
bexmarilimab
Galera earns key FDA designation for pancreatic cancer drug
Clinical Trials Arena
Fri, 05/19/23 - 11:29 am
Galera Therapeutics
pancreatic cancer
FDA
rucosopasem
orphan drugs
SiSaf gets green light from FDA for osteopetrosis treatment
Biopharma Reporter
Mon, 05/15/23 - 10:16 am
SiSaf
orphan drugs
pediatric
FDA
osteopetrosis
SIS-101-ADO
GSK receives orphan drug designation for Benlysta to treat systemic sclerosis
Pharmaceutical Business Review
Thu, 02/2/23 - 10:25 am
GSK
FDA
orphan drugs
Benlysta
systemic sclerosis
FDA restores orphan-exclusivity system after 18-month stall in wake of legal feud
Medical Marketing and Media
Tue, 01/31/23 - 11:25 pm
FDA
orphan drugs
exclusivity
Here Are the Top Five Biotech Trends for 2023
NASDAQ
Mon, 12/19/22 - 11:23 am
biotech
personalized medicine
bioprinting
tissue engineering
orphan drugs
drug discovery
gene editing
CRISPR
FDA remains silent on orphan drug exclusivity after last year's court loss
Endpoints
Thu, 12/1/22 - 07:09 pm
FDA
orphan drug exclusivity
orphan drugs
Intellia's CRISPR-engineered cell therapy secures FDA orphan drug status after AML trial launch
Fierce Biotech
Wed, 03/9/22 - 11:13 pm
Intellia Therapeutics
CRISPR
FDA
cell therapy
orphan drugs
Biliary tract cancer drug granted orphan drug designation in US
Pharmaforum
Fri, 01/21/22 - 10:56 am
Senhwa
biliary tract cancer
silmitasertib
FDA
orphan drugs
Celularity Gains FDA Orphan Drug Status on Strength of Placental Stem Cell Trials
BioSpace
Wed, 04/14/21 - 09:35 am
Celularity
FDA
orphan drugs
natural killer cells
malignant glioma
Bill to close orphan drug loophole clears House
Beckers Hospital Review
Wed, 11/18/20 - 10:54 pm
legislation
orphan drugs
Sanofi grapples with rejection of potential first-in-class orphan drug, faults third-party manufacturing
Endpoints
Mon, 11/16/20 - 10:25 am
Sanofi
sutimlimab
orphan drugs
FDA
drug manufacturing
Forma Therapeutics gets European orphan drug status for FT-4202 to treat sickle cell disease
Pharmaceutical Business Review
Thu, 11/12/20 - 10:40 am
Forma Therapeutics
orphan drugs
Europe
FT-4202
sickle cell disease
Orphan drug incentives reviewed at BIO
RAPS.org
Tue, 06/9/20 - 11:25 pm
BIO 2020
orphan drugs
drug development
Gilead Asks the FDA to Rescind Orphan Drug Designation for Remdesivir as a Treatment for COVID-19
Motley Fool
Wed, 03/25/20 - 11:59 pm
Gilead Sciences
remdesivir
FDA
orphan drugs
COVID-19
The biggest challenges facing rare disease pharma – and how the industry can tackle them
Pharmaforum
Sat, 02/29/20 - 07:17 pm
Rare Diseases
orphan drugs
drug development
FDA
drug pricing
AstraZeneca’s Combination Treatment for HCC Snags Orphan Drug Designation
BioSpace
Mon, 01/20/20 - 10:16 pm
AstraZeneca
Imfinzi
orphan drugs
FDA
hepatocellular carcinoma

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