PKU

Synlogic shuts down after PKU drug fails phase 3 trial
Pharmaphorum
Fri, 02/9/24 - 11:11 am
Synlogic
PKU
clinical trials
Gene editing biotech Homology hits reset and seeks a sale
BioPharma Dive
Fri, 07/28/23 - 10:35 am
Homology
PKU
gene editing
M&A
PTC, chasing BioMarin, posts phase 3 rare disease win but fails to silence skeptics
Fierce Biotech
Thu, 05/18/23 - 10:59 am
PTC Therapeutics
Biomarin
PKU
clinical trials
Another phenylketonuria hold, courtesy of Homology
EP Vantage
Tue, 02/22/22 - 10:43 am
Homology Medicines
HMI-102
Biomarin
BMN 307
FDA
clinical trials
clinical hold
PKU
FDA grounds BioMarin gene therapy trial for months with demand for tumor risk data
Fierce Biotech
Fri, 02/18/22 - 10:32 am
Biomarin
FDA
clinical trials
clinical hold
BMN 307
PKU
gene therapy
Pfizer invests in Homology and adds to its gene therapy ambitions
BioPharma Dive
Tue, 11/10/20 - 11:08 am
Pfizer
gene therapy
PKU
Homology Medicines
Stepping on BioMarin's turf, PTC Therapeutics picks up PKU drug for a song
Endpoints
Thu, 05/7/20 - 10:42 am
PTC Therapeutics
Censa Pharmaceuticals
PKU
M&A
Rubius delays first clinical readout, as crowded PKU field marches on
Biopharma Dive
Thu, 11/14/19 - 07:40 pm
Rubius
PKU
clinical trials
RTX-134
Synlogic Presents Data Describing a Solid Oral Formulation for Synthetic Biotic Medicine for the Treatment of PKU
CP Wire
Fri, 05/3/19 - 09:49 am
Synlogic
SYNB1618
PKU
Synlogic Presents Data Describing a Solid Oral Formulation for Synthetic Biotic Medicine for the Treatment of PKU
Thu, 05/2/19 - 11:51 am
Synlogic
SYNB1618
PKU
Pre-clinical Data Supports Synlogic's Synthetic Biotic as a Potential Treatment for Phenylketonuria
CP Wire
Tue, 08/14/18 - 12:09 am
Synlogic
SYNB1618
microbiome
PKU
Pre-clinical Data Supports Synlogic's Synthetic Biotic as a Potential Treatment for Phenylketonuria
Mon, 08/13/18 - 11:54 pm
Synlogic
SYNB1618
microbiome
PKU
BioMarin Rises on Approval of Palynziq (pegvaliase-pqpz)
CP Wire
Fri, 05/25/18 - 09:15 am
Biomarin
Palynziq
PKU
FDA
BioMarin Rises on Approval of Palynziq (pegvaliase-pqpz)
Fri, 05/25/18 - 08:45 am
Biomarin
Palynziq
PKU
A Big Decision Is Fast-Approaching for This Rare-Disease Drugmaker
Motley Fool
Wed, 05/23/18 - 03:06 pm
Biomarin
pegvaliase
PKU
FDA
BioMarin Cruises While It Waits on Seventh Approval
Motley Fool
Fri, 04/27/18 - 08:15 pm
Biomarin
pegvaliase
FDA
PKU
earnings
BioMarin Receives Notice of Allowance for Once Daily Dosing Patent for Kuvan
Yahoo
Mon, 03/30/09 - 09:16 am
Biomarin
Kuvan
PKU
BioMarin a Buy with a $28 Target
Yahoo/Zacks.com
Tue, 01/6/09 - 04:54 pm
Biomarin
Aldurazyme
Kuvan
PKU