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clinical trials
Pfizer gene therapy for Duchenne fails to meet goals of key trial
BioPharma Dive
Wed, 06/12/24 - 11:32 pm
Pfizer
Duchenne Muscular Dystrophy
DMD
clinical trials
Ciffreo
Alzheimer’s Drug Developer Alzheon Closes $100M Series E Financing
Genetic Engineering News
Wed, 06/12/24 - 11:29 pm
Alzheon
clinical trials
funding
Alzheimer's disease
valiltramiprosate
Cara Therapeutics discontinues neurological condition study as drug fails
Reuters
Wed, 06/12/24 - 11:21 pm
Cara Therapeutics
clinical trials
Notalgia paresthetica
difelikefalin
Early data for Avidity's RNA therapy show possible functional benefit in muscular dystrophy
Fierce Biotech
Wed, 06/12/24 - 11:19 pm
Avidity Biosciences
RNA
AOC 1020
del-brax
FSHD
clinical trials
Sage’s Dalzanemdor Shows Effect in Huntington’s Study, Analysts Say Results ‘Underwhelming’
BioSpace
Tue, 06/11/24 - 10:51 pm
SAGE Therapeutics
dalzanemdor
clinical trials
Huntington's disease
DCTs no longer? Decentralized solutions in post-pandemic clinical trials
Clinical Trials Arena
Tue, 06/11/24 - 11:17 am
clinical trials
decentralized clinical trials
pandemic
Skye Nixes Eye Disease Drug After Phase II Failure, Focuses on Metabolic Program
BioSpace
Mon, 06/10/24 - 05:49 pm
Skye Bioscience
SBI-100
clinical trials
glaucoma
Moderna’s COVID-Flu combo shot beats separate vaccines in phase III study
BioSpace
Mon, 06/10/24 - 11:27 am
Moderna Therapeutics
clinical trials
mRNA-1083
vaccines
COVID-19
Flu
Roche’s Evrysdi offers sustained benefits in SMA extension trial in children
Clinical Trials Arena
Mon, 06/10/24 - 11:06 am
Roche
clinical trials
Evrysdi
SMA
Diabetes biotech stock Biomea tanks as FDA imposes full clinical hold
Fierce Biotech
Fri, 06/7/24 - 11:22 am
Biomea Fusion
FDA
clinical trials
diabetes
BMF-219
Melt doses first subject in Phase III trial of non-opioid sedation tablet
Clinical Trials Arena
Fri, 06/7/24 - 11:11 am
Melt Pharmaceuticals
clinical trials
MELT-300
cataract surgery
Boehringer, Zealand’s GLP-1 MASH Data ‘Unintentionally’ Published by Medical Congress Website
BioSpace
Thu, 06/6/24 - 11:48 am
Zealand Pharma
Boehringer Ingelheim
MASH
survodutide
clinical trials
AbbVie treats first subject in Phase III multiple myeloma drug trial
Clinical Trials Arena
Thu, 06/6/24 - 11:31 am
AbbVie
clinical trials
ABBV-383
Multiple Myeloma
Lilly’s Tirzepatide Shows Positive Phase II NASH Data, Tees Up Potential Expansion
BioSpace
Wed, 06/5/24 - 11:08 am
Eli Lilly
NASH
MASH
clinical trials
tirzepatide
Amgen's drug meets main goal in late-stage study for rare disease
Reuters
Wed, 06/5/24 - 11:03 am
Amgen
clinical trials
Uplinza
IgG4-RD
Vir pressures Gilead with hepatitis D cocktail showing early efficacy in phase 2
Fierce Biotech
Wed, 06/5/24 - 11:01 am
Vir Biotechnology
hepatitis D
clinical trials
Gilead Sciences
Annexon's neurological disease drug succeeds in late-stage study
Reuters
Tue, 06/4/24 - 11:46 am
Annexon
clinical trials
Guillain-Barré Syndrome
ANX005
Bayer taps Samsung wearables for menopause sleep study
Pharmaphorum
Tue, 06/4/24 - 11:31 am
Bayer
Samsung
wearables
Medtech
menopause
clinical trials
GSK’s Jemperli shows potential in Phase II trial for locally advanced rectal cancer
Clinical Trials Arena
Tue, 06/4/24 - 11:26 am
GSK
Jemperli
clinical trials
rectal cancer
Agios Blood Disorder Drug Scores Another Phase III Win
BioSpace
Mon, 06/3/24 - 10:47 pm
Agios Pharmaceuticals
Pyrukynd
clinical trials
transfusion-dependent alpha- or beta-thalassemia
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