Early data for Avidity's RNA therapy show possible functional benefit in muscular dystrophy

Early data for Avidity's RNA therapy show possible functional benefit in muscular dystrophy

Source: 
Fierce Biotech
snippet: 

Avidity Biosciences’ AOC 1020, newly dubbed del-brax, demonstrated a safe profile and was tied to functional improvement among people with facioscapulohumeral muscular dystrophy (FSHD) in a phase 1/2 trial.