Patient Death Likely from Virus Used to Deliver Gene-Editing Therapy: NEJM Study

Patient Death Likely from Virus Used to Deliver Gene-Editing Therapy: NEJM Study

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BioSpace
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A paper published on Thursday in The New England Journal of Medicine suggests that the potential cause of the 2022 death of a Duchenne muscular dystrophy patient was due to an innate immune reaction triggered by the high dose of recombinant adeno-associated virus used to deliver the gene therapy.