Duchenne Muscular Dystrophy

Solid Bio Restructures to Get Halted Gene Therapy Study Back on Track
Solid Bio Restructures to Get Halted Gene Therapy Study Back on Track
Xconomy
Solid Biosciences
gene therapy
reorganization
Duchenne Muscular Dystrophy
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Roche Puts Up Historic $1.15B for Sarepta Duchenne Gene Therapy Deal
Roche Puts Up Historic $1.15B for Sarepta Duchenne Gene Therapy Deal
Xconomy
Roche
Sarepta Therapeutics
FDA
Duchenne Muscular Dystrophy
SRP-9001
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Wave Stock Crashes After Decision to Halt Duchenne Drug Studies
Wave Stock Crashes After Decision to Halt Duchenne Drug Studies
Xconomy
Wave Life Sciences
Duchenne Muscular Dystrophy
suvodirsen
clinical trials
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3 Biotech Stocks With Big Incoming Catalysts
3 Biotech Stocks With Big Incoming Catalysts
Motley Fool
Axsome Therapeutics
AXS-05
Solid Biosciences
SGT-001
Duchenne Muscular Dystrophy
major depressive disorder
Intra-Cellular Therapies
lumateperone
schizophrenia
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In stunning twist, FDA approves Sarepta's Duchenne drug it rejected
In stunning twist, FDA approves Sarepta's Duchenne drug it rejected
Biopharma Dive
FDA
Sarepta Therapeutics
Duchenne Muscular Dystrophy
Vyondys 53
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Wave faces key test in bid to challenge Sarepta in DMD
Wave faces key test in bid to challenge Sarepta in DMD
Biopharma Dive
Wave Life Sciences
Sarepta Therapeutics
Exondys 51
Duchenne Muscular Dystrophy
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Solid Biosciences’ Duchenne gene therapy trial halted after patient suffers serious toxicity
Solid Biosciences’ Duchenne gene therapy trial halted after patient suffers serious toxicity
Stat
Solid Biosciences
Duchenne Muscular Dystrophy
clinical trials
gene therapy
FDA
SGT-001
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Roche joins others in dropping myostatin inhibitor for DMD
Roche joins others in dropping myostatin inhibitor for DMD
Pharmaforum
Roche
Duchenne Muscular Dystrophy
RG6206
myostatin inhibitors
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Sarepta Therapeutics CEO playing nice with FDA over rejection of Duchenne drug
Sarepta Therapeutics CEO playing nice with FDA over rejection of Duchenne drug
Stat
Sarepta Therapeutics
Doug Ingram
FDA
Vyondys 53
Duchenne Muscular Dystrophy
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Sarepta competitor files with FDA for Duchenne drug
Sarepta competitor files with FDA for Duchenne drug
Seeking Alpha
Sarepta Therapeutics
NS Pharma
golodirsen
FDA
Duchenne Muscular Dystrophy
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Wave takes a different tack from Sarepta in Duchenne
Wave takes a different tack from Sarepta in Duchenne
EP Vantage
Wave Life Sciences
Duchenne Muscular Dystrophy
suvodirsen
Sarepta Therapeutics
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The FDA and Sarepta: a window into the real world of drug regulation
The FDA and Sarepta: a window into the real world of drug regulation
Stat
FDA
regulatory
Sarepta Therapeutics
Duchenne Muscular Dystrophy
Exondys 51
Vyondys 53
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Santhera's Duchenne effort gets a boost on positive PhIIa for alternative steroid vamorolone — though there's a lot left to prove
Santhera's Duchenne effort gets a boost on positive PhIIa for alternative steroid vamorolone — though there's a lot left to prove
Endpoints
Santhera
Duchenne Muscular Dystrophy
clinical trials
vamorolone
RaveraGen
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Sarepta now needs flawless progress for gene therapy
Sarepta now needs flawless progress for gene therapy
Biopharma Dive
Sarepta Therapeutics
FDA
Duchenne Muscular Dystrophy
Vyondys 53
gene therapy
SRP-9001
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Sarepta Duchenne drug rejected by FDA in surprise decision
Sarepta Duchenne drug rejected by FDA in surprise decision
Biopharma Dive
Sarepta Therapeutics
Duchenne Muscular Dystrophy
FDA
complete response letter
Vyondys 53
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Solid Biosciences Surges on DMD Gene Therapy Study Amendments
Solid Biosciences Surges on DMD Gene Therapy Study Amendments
Yahoo/Zacks.com
Solid Biosciences
SGT-001
Duchenne Muscular Dystrophy
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Sarepta's Lone Analyst Skeptic Takes On 22 Bulls With Renewed Warnings
Sarepta's Lone Analyst Skeptic Takes On 22 Bulls With Renewed Warnings
Bloomberg
Sarepta Therapeutics
analysts
Duchenne Muscular Dystrophy
Vyondys 53
Exondys 51
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Patient in Sarepta gene therapy trial develops serious illness; shares plunge
Patient in Sarepta gene therapy trial develops serious illness; shares plunge
Yahoo/Reuters
Sarepta Therapeutics
Duchenne Muscular Dystrophy
rhabdomyolysis
gene therapy
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Studies Show Sarepta's Exondys 51 Slows Respiratory Decline in Muscular Dystrophy Patients
Studies Show Sarepta's Exondys 51 Slows Respiratory Decline in Muscular Dystrophy Patients
BioSpace
Sarepta Therapeutics
Exondys 51
DMD
Duchenne Muscular Dystrophy
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Pfizer's DMD Gene Therapy Shows Severe Side Effects in Study
Pfizer's DMD Gene Therapy Shows Severe Side Effects in Study
Yahoo/Zacks.com
Pfizer
DMD
Duchenne Muscular Dystrophy
clinical trials
gene therapy
PF-06939926
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