Duchenne Muscular Dystrophy

Sarepta bags drug to fully unlock DMD gene therapy opportunity
Sarepta bags drug to fully unlock DMD gene therapy opportunity
Fierce Biotech
Sarepta Therapeutics
Duchenne Muscular Dystrophy
Hansa Biopharma
gene therapy
Flag link:
OptumRx: The 3 drugs that will have the biggest impact on payers, patients in 2020
OptumRx: The 3 drugs that will have the biggest impact on payers, patients in 2020
Beckers Hospital Review
OptumRx
Roche
PTC Therapeutics
risdiplam
SMA
NS Pharma
viltolarsen
Duchenne Muscular Dystrophy
Immunomedics
Trodelvy
triple negative breast cancer
Flag link:
Safety questions linger as Pfizer preps Duchenne gene therapy for final test
Safety questions linger as Pfizer preps Duchenne gene therapy for final test
BioPharma Dive
Pfizer
gene therapy
Duchenne Muscular Dystrophy
PF-06939926
Flag link:
One year on, Capricor's stem cell therapy appears to help DMD patients in small study, but investors balk at the data
One year on, Capricor's stem cell therapy appears to help DMD patients in small study, but investors balk at the data
Endpoints
Capricor
stem cells
Duchenne Muscular Dystrophy
CAP-1002
Flag link:
Wave Life Sciences hits tumultuous waters as ax comes crashing down on staffers
Wave Life Sciences hits tumultuous waters as ax comes crashing down on staffers
Fierce Biotech
Wave Life Sciences
layoffs
Duchenne Muscular Dystrophy
Flag link:
FDA Flags Risk of Infection, Kidney Damage for Sarepta Duchenne Drugs
FDA Flags Risk of Infection, Kidney Damage for Sarepta Duchenne Drugs
Xconomy
Sarepta Therapeutics
Vyondys 53
Duchenne Muscular Dystrophy
FDA
Flag link:
Solid Bio Restructures to Get Halted Gene Therapy Study Back on Track
Solid Bio Restructures to Get Halted Gene Therapy Study Back on Track
Xconomy
Solid Biosciences
gene therapy
reorganization
Duchenne Muscular Dystrophy
Flag link:
Roche Puts Up Historic $1.15B for Sarepta Duchenne Gene Therapy Deal
Roche Puts Up Historic $1.15B for Sarepta Duchenne Gene Therapy Deal
Xconomy
Roche
Sarepta Therapeutics
FDA
Duchenne Muscular Dystrophy
SRP-9001
Flag link:
Wave Stock Crashes After Decision to Halt Duchenne Drug Studies
Wave Stock Crashes After Decision to Halt Duchenne Drug Studies
Xconomy
Wave Life Sciences
Duchenne Muscular Dystrophy
suvodirsen
clinical trials
Flag link:
3 Biotech Stocks With Big Incoming Catalysts
3 Biotech Stocks With Big Incoming Catalysts
Motley Fool
Axsome Therapeutics
AXS-05
Solid Biosciences
SGT-001
Duchenne Muscular Dystrophy
major depressive disorder
Intra-Cellular Therapies
lumateperone
schizophrenia
Flag link:
In stunning twist, FDA approves Sarepta's Duchenne drug it rejected
In stunning twist, FDA approves Sarepta's Duchenne drug it rejected
Biopharma Dive
FDA
Sarepta Therapeutics
Duchenne Muscular Dystrophy
Vyondys 53
Flag link:
Wave faces key test in bid to challenge Sarepta in DMD
Wave faces key test in bid to challenge Sarepta in DMD
Biopharma Dive
Wave Life Sciences
Sarepta Therapeutics
Exondys 51
Duchenne Muscular Dystrophy
Flag link:
Solid Biosciences’ Duchenne gene therapy trial halted after patient suffers serious toxicity
Solid Biosciences’ Duchenne gene therapy trial halted after patient suffers serious toxicity
Stat
Solid Biosciences
Duchenne Muscular Dystrophy
clinical trials
gene therapy
FDA
SGT-001
Flag link:
Roche joins others in dropping myostatin inhibitor for DMD
Roche joins others in dropping myostatin inhibitor for DMD
Pharmaforum
Roche
Duchenne Muscular Dystrophy
RG6206
myostatin inhibitors
Flag link:
Sarepta Therapeutics CEO playing nice with FDA over rejection of Duchenne drug
Sarepta Therapeutics CEO playing nice with FDA over rejection of Duchenne drug
Stat
Sarepta Therapeutics
Doug Ingram
FDA
Vyondys 53
Duchenne Muscular Dystrophy
Flag link:
Sarepta competitor files with FDA for Duchenne drug
Sarepta competitor files with FDA for Duchenne drug
Seeking Alpha
Sarepta Therapeutics
NS Pharma
golodirsen
FDA
Duchenne Muscular Dystrophy
Flag link:
Wave takes a different tack from Sarepta in Duchenne
Wave takes a different tack from Sarepta in Duchenne
EP Vantage
Wave Life Sciences
Duchenne Muscular Dystrophy
suvodirsen
Sarepta Therapeutics
Flag link:
The FDA and Sarepta: a window into the real world of drug regulation
The FDA and Sarepta: a window into the real world of drug regulation
Stat
FDA
regulatory
Sarepta Therapeutics
Duchenne Muscular Dystrophy
Exondys 51
Vyondys 53
Flag link:
Santhera's Duchenne effort gets a boost on positive PhIIa for alternative steroid vamorolone — though there's a lot left to prove
Santhera's Duchenne effort gets a boost on positive PhIIa for alternative steroid vamorolone — though there's a lot left to prove
Endpoints
Santhera
Duchenne Muscular Dystrophy
clinical trials
vamorolone
RaveraGen
Flag link:
Sarepta now needs flawless progress for gene therapy
Sarepta now needs flawless progress for gene therapy
Biopharma Dive
Sarepta Therapeutics
FDA
Duchenne Muscular Dystrophy
Vyondys 53
gene therapy
SRP-9001
Flag link:

Pages