DMD

FDA Reverses Course; Will Hold Adcomm for Sarepta’s DMD Gene Therapy
FDA Reverses Course; Will Hold Adcomm for Sarepta’s DMD Gene Therapy
BioSpace
FDA
Sarepta Therapeutics
DMD
gene therapy
Duchenne Muscular Dystrophy
SRP-9001
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Duchenne muscular dystrophy: major trials and events to watch in 2023
Duchenne muscular dystrophy: major trials and events to watch in 2023
Clinical Trials Arena
DMD
Duchenne Muscular Dystrophy
clinical trials
gene therapy
FDA
Sarepta Therapeutics
SRP-9001
FibroGen
pamrevlumab
Capricor
CAP-1002
Santhera
ReveraGen
vamorolone
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Sarepta: FDA finds ‘no significant safety issues of concern’ with DMD gene therapy
Sarepta: FDA finds ‘no significant safety issues of concern’ with DMD gene therapy
Biopharma Reporter
Sarepta Therapeutics
DMD
Duchenne Muscular Dystrophy
gene therapy
FDA
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Sarepta's DMD gene therapy inches closer to market as FDA declines to hold advisory meeting
Sarepta's DMD gene therapy inches closer to market as FDA declines to hold advisory meeting
Fierce Biotech
FDA
Sarepta Therapeutics
SRP-9001
gene therapy
DMD
Duchenne Muscular Dystrophy
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Vertex tiptoes further into Duchenne research with Tevard deal
Vertex tiptoes further into Duchenne research with Tevard deal
BioPharma Dive
Vertex Pharmaceuticals
Duchenne Muscular Dystrophy
DMD
Tevard Biosciences
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Duchenne muscular dystrophy’s progress so far in 2023
Duchenne muscular dystrophy’s progress so far in 2023
Clinical Trials Arena
Duchenne Muscular Dystrophy
DMD
Santhera Pharmaceuticals
ReveraGen
vamorolone
Regenxbio
RGX-202
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Buoyed by new data, Santhera preps filing for DMD drug vamorolone
Buoyed by new data, Santhera preps filing for DMD drug vamorolone
Pharmaforum
Santhera
DMD
Duchenne Muscular Dystrophy
idebenone
vamorolone
FDA
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Biotechs Fly Sideways In Quiet Week — 5 News Items You May Have Missed
Biotechs Fly Sideways In Quiet Week — 5 News Items You May Have Missed
Investors Business Daily
Wave Life Sciences
suvodirsen
DMD
Merck
Keytruda
Biogen
Spinraza
Zoetis
Europe
animal health
Jazz Pharmaceuticals
JZP-258
narcolepsy
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Studies Show Sarepta's Exondys 51 Slows Respiratory Decline in Muscular Dystrophy Patients
Studies Show Sarepta's Exondys 51 Slows Respiratory Decline in Muscular Dystrophy Patients
BioSpace
Sarepta Therapeutics
Exondys 51
DMD
Duchenne Muscular Dystrophy
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Pfizer's DMD Gene Therapy Shows Severe Side Effects in Study
Pfizer's DMD Gene Therapy Shows Severe Side Effects in Study
Yahoo/Zacks.com
Pfizer
DMD
Duchenne Muscular Dystrophy
clinical trials
gene therapy
PF-06939926
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Gene Therapy vs. Gene Editing: Which Is Better for Tackling Muscular Dystrophy?
Gene Therapy vs. Gene Editing: Which Is Better for Tackling Muscular Dystrophy?
Motley Fool
gene editing
gene therapy
DMD
Duchenne Muscular Dystrophy
Vertex Pharmaceuticals
CRISPR Therapeutics
Exonics
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Vertex sets sights on DMD gene therapy, joining crowded field
Vertex sets sights on DMD gene therapy, joining crowded field
Biopharma Dive
Vertex Pharmaceuticals
DMD
M&A
CRISPR Therapeutics
Exonics
gene therapy
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CRISPR corrects DMD in mice for a year in Sarepta-supported study
CRISPR corrects DMD in mice for a year in Sarepta-supported study
Fierce Biotech
Duke University
Sarepta Therapeutics
CRISPR
gene editing
DMD
Duchenne Muscular Dystrophy
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Down but Not Out: 10 Biggest Drug Trials That Saw Challenges in 2018
Down but Not Out: 10 Biggest Drug Trials That Saw Challenges in 2018
BioSpace
clinical trials
Takeda
Zinfandel Pharmaceuticals
pioglitazone
Alzheimer's disease
Boehringer Ingelheim
BI 409306
Merck
verubecestat
Celgene
MS
ozanimod
Incyte
ID01
melanoma
vTv Therapeutics
azeliragon
Roche
Tecentriq
Exelixis
colorectal cancer
JNJ
atabacestat
Sareptat Therapeutics
DMD
Exondys 51
Alkermes
ALKS-5461
clinical depression
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Researchers Use CRISPR to Treat Duchenne Muscular Dystrophy in Dogs
Researchers Use CRISPR to Treat Duchenne Muscular Dystrophy in Dogs
BioSpace
DMD
Duchenne Muscular Dystrophy
CRISPR
drug development
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Solid Bio's DMD gene therapy graduates from partial FDA hold to full-on clinical hold
Solid Bio's DMD gene therapy graduates from partial FDA hold to full-on clinical hold
Fierce Biotech
Solid Biosciences
gene therapy
FDA
DMD
Duchenne Muscular Dystrophy
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Did the FDA just leave the door cracked open for PTC’s Duchenne drug after repeated slapdowns?
Did the FDA just leave the door cracked open for PTC’s Duchenne drug after repeated slapdowns?
Endpoints
FDA
PTC Therapeutics
DMD
Duchenne Muscular Dystrophy
ataluren
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Data from trials could send these clinical-stage biotech stocks soaring or crashing
Data from trials could send these clinical-stage biotech stocks soaring or crashing
Motley Fool
clinical trials
biotech
Summit Therapeutics
DMD
Jounce Therapeutics
JTX-2011
TG Therapeutics
ublituximab
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Delayed FDA Decision Sends Sarepta Therapeutics Soaring
Delayed FDA Decision Sends Sarepta Therapeutics Soaring
Yahoo/Market Realist
Sarepta Therapeutics
DMD
FDA
eteplirsen
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