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gene therapy

Neurogene Launches With $68.5 Million to Advance Gene Therapies for Rare Neurological Diseases

Neurogene Launches With $68.5 Million to Advance Gene Therapies for Rare Neurological Diseases

BioSpace

neurological disorders

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J&J snags rights to a gene therapy portfolio from little MeiraGTx, a spinoff from Sam Waksal’s Kadmon

J&J snags rights to a gene therapy portfolio from little MeiraGTx, a spinoff from Sam Waksal’s Kadmon

Endpoints

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Novartis: Alternative payments will ‘reset the paradigm’ for covering gene, cell therapies

Novartis: Alternative payments will ‘reset the paradigm’ for covering gene, cell therapies

Fierce Pharma

spinal muscular atrophy

alternative payments

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Neurocrine Pays $165M to Bankroll Voyager’s Gene Therapy for Parkinson’s

Neurocrine Pays $165M to Bankroll Voyager’s Gene Therapy for Parkinson’s

Xconomy

Voyager Therapeutics

Parkinson's Disease

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Moment of truth for Sarepta and Myonexus

Moment of truth for Sarepta and Myonexus

EP Vantage

Sarepta Therapeutics

Limb Girdle Muscular Dystrophy

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Gottlieb, Marks detail plans to advance development of cell and gene therapies

Gottlieb, Marks detail plans to advance development of cell and gene therapies

Endpoints

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Massachusetts Initiative Looks at Payment Plans for Novartis' SMA Gene Therapy

Massachusetts Initiative Looks at Payment Plans for Novartis' SMA Gene Therapy

BioSpace

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Lilly eyes more cancer deals, but wary of CAR-T, gene therapy

Lilly eyes more cancer deals, but wary of CAR-T, gene therapy

Yahoo/Reuters

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JPM19: Spark looks at scale, manufacturing as gene therapy matures

JPM19: Spark looks at scale, manufacturing as gene therapy matures

Biopharma Dive

Spark Therapeutics

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Ex-Juno execs launch cell therapy start-up Sana

Ex-Juno execs launch cell therapy start-up Sana

BioCentury

Sana Biotechnology

Juno Therapeutics

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Sarepta inks deal to bolster gene therapy manufacturing

Sarepta inks deal to bolster gene therapy manufacturing

Biopharma Dive

Sarepta Therapeutics

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Orphan Drug Designation Granted to Investigational Gene Therapy for Rare Form of Muscular Dystrophy

Orphan Drug Designation Granted to Investigational Gene Therapy for Rare Form of Muscular Dystrophy

CP Wire

Limb Girdle Muscular Dystrophy

muscular dystrophy

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Biogen backs away from AGTC after gene therapy failure

Biogen backs away from AGTC after gene therapy failure

BioPharma Dive

Applied Genetic Technologies

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Biogen bails on AGTC after ocular gene therapy flunks trial

Biogen bails on AGTC after ocular gene therapy flunks trial

Fierce Biotech

Applied Genetic Technologies

rAAV2tYF-CB-hRS1

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Axovant axes neuroscience drug, focuses on gene therapies

Axovant axes neuroscience drug, focuses on gene therapies

Pharmaforum

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Angina gene therapy company XyloCor raises $17M series A round

Angina gene therapy company XyloCor raises $17M series A round

BioCentury

XyloCor Therapeutics

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Nearly 300 gene and cell therapies in development – report

Nearly 300 gene and cell therapies in development – report

Pharmaforum

drug development

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Novartis’ SMA Gene Therapy Is on the Fast Track for Approval

Novartis’ SMA Gene Therapy Is on the Fast Track for Approval

BioSpace

priority review

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Novartis CEO Vas Narasimhan On The Price Of Gene Therapies: 'It's A Challenge We Have To Solve'

Novartis CEO Vas Narasimhan On The Price Of Gene Therapies: 'It's A Challenge We Have To Solve'

Forbes

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Biotech Showcase Conference Reveals Six Therapeutic Areas Receiving the Most Investment Attention in 2019

Biotech Showcase Conference Reveals Six Therapeutic Areas Receiving the Most Investment Attention in 2019

CP Wire

Alzheimer's disease

immuno-oncology

orphan diseases

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