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gene therapy

BioMarin sets gene therapy sights beyond hemophilia

BioMarin sets gene therapy sights beyond hemophilia

BioPharma Dive

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Generation Bio Pockets $110M for Next Wave of Gene Therapy, IPO Plans

Generation Bio Pockets $110M for Next Wave of Gene Therapy, IPO Plans

Xconomy

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Ultragenyx shares jump on 'better than expected' gene therapy data

Ultragenyx shares jump on 'better than expected' gene therapy data

Fierce Biotech

clinical trials

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Solid Bio Restructures to Get Halted Gene Therapy Study Back on Track

Solid Bio Restructures to Get Halted Gene Therapy Study Back on Track

Xconomy

Solid Biosciences

Duchenne Muscular Dystrophy

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3 trends in biotech to watch in 2020

3 trends in biotech to watch in 2020

Stat

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Pharma's gene and cell therapy ambitions will kick into high gear in 2020—despite some major hurdles

Pharma's gene and cell therapy ambitions will kick into high gear in 2020—despite some major hurdles

Fierce Pharma

drug manufacturing

Bristol-Myers Squibb

Sarepta Therapeutics

Gilead Sciences

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Zolgensma for free? Yes, but advocates worry about Novartis' lottery-style giveaway

Zolgensma for free? Yes, but advocates worry about Novartis' lottery-style giveaway

Fierce Pharma

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Value-based pricing for gene therapy? Maybe not ready for hemophilia

Value-based pricing for gene therapy? Maybe not ready for hemophilia

Biopharma Dive

valoctocogene roxaparvovec

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Hopkins team invents non-viral system for getting gene therapy into cells

Hopkins team invents non-viral system for getting gene therapy into cells

Fierce Biotech

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Limelight Bio emerges with $75m to develop next generation gene therapies to overcome limitations of current treatments

Limelight Bio emerges with $75m to develop next generation gene therapies to overcome limitations of current treatments

Pharmaceutical Business Review

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FerGene’s Bladder Cancer Phase III Trial Hits Its Mark

FerGene’s Bladder Cancer Phase III Trial Hits Its Mark

BioSpace

Ferring Pharmaceuticals

Blackstone Life Sciences

clinical trials

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Here's Why BioMarin Pharmaceutical Leapt 10.2% in November

Here's Why BioMarin Pharmaceutical Leapt 10.2% in November

Motley Fool

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Gene Therapy M&A Appetite Provides Lift After Audentes Deal

Gene Therapy M&A Appetite Provides Lift After Audentes Deal

Yahoo/Bloomberg

Audentes Therapeutics

Medicines Company

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Merck's Keytruda is bound for new bladder cancer territory. But can it hold up against gene therapy?

Merck's Keytruda is bound for new bladder cancer territory. But can it hold up against gene therapy?

Fierce Pharma

nadofaragene firadenovec

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Japan's Astellas to buy Audentes for $3 billion in gene therapy push

Japan's Astellas to buy Audentes for $3 billion in gene therapy push

Reuters

Audentes Therapeutics

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3 Soaring Biotech Stocks to Watch in December

3 Soaring Biotech Stocks to Watch in December

Motley Fool

Arrowhead Pharmaceuticals

Adverum Biotechnologies

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Novartis opens new cell and gene therapies facility in Switzerland

Novartis opens new cell and gene therapies facility in Switzerland

Pharmaceutical Business Review

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Pfizer, Novartis lead $2 billion spending spree on gene therapy production

Pfizer, Novartis lead $2 billion spending spree on gene therapy production

Reuters

drug manufacturing

PTC Therapeutics

Krystal Biotech

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2 Small-Cap Biotechs That Soared Last Week

2 Small-Cap Biotechs That Soared Last Week

Motley Fool

Magenta Therapeutics

Molecular Templates

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$50M cell and viral vector manufacturing operation backed by Harvard

$50M cell and viral vector manufacturing operation backed by Harvard

Fierce Pharma

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