Pompe disease

Amicus Announces Positive Results for AT-GAA in Pompe Disease
Fri, 10/5/18 - 09:46 am
Amicus Therapeutics
AT-GAA
Pompe disease
FDA kills off Amicus’ 2018 accelerated approval plan
Fierce Biotech
Mon, 09/10/18 - 09:52 am
FDA
Amicus Therapeutics
Pompe disease
AT-GAA
Sarepta all-in on gene therapy pipeline, adding 3 CNS treatments in $30M Lacerta deal
Endpoints
Wed, 08/8/18 - 10:42 pm
Sarepta Therapeutics
CNS
Pompe disease
Lacerta
Pompe Disease Patients on Amicus Drug Continue to Improve in Study
Xconomy
Wed, 02/7/18 - 10:11 pm
Pompe disease
Amicus
ABT200
Amicus’ latest positive update on Pompe drug hints at accelerated approval pitch
Endpoints
Wed, 10/4/17 - 11:15 am
Amicus Therapeutics
Pompe disease
ATB200/AT2221
Sanofi Genzyme to begin late-stage trial of new drug for Pompe disease by summer
Bizjournals.com
Fri, 03/4/16 - 02:21 pm
Sanofi Genzyme
Pompe disease
clinical trials
NeoGAA
BioMarin says it will continue studies of late-onset Pompe disease drug candidate BMN-701
Yahoo/AP
Wed, 03/20/13 - 12:26 pm
Biomarin
Pompe disease
BMN-701
Amicus Therapeutics: One Biotech Firm Making Considerable Strides In Terms Of Pompe Disease
Seeking Alpha
Sat, 01/5/13 - 10:50 am
Amicus Therapeutics
biotech
Pompe disease
Amicus Theraputics announces positive results from Phase 2 Chaperone-ERT study
The Fly on the Wall
Fri, 01/4/13 - 11:32 am
Amicus Therapeutics
AT2220
Pompe disease
Will The Sanofi Pompe Paradigm Play Out With Neuralstem And Lou Gehrig's Disease?
Seeking Alpha
Fri, 10/5/12 - 12:05 pm
Pompe disease
Sanofi
Neuralstem
Lou Gehrig's disease
Piper Jaffray Boosts Target on BioMarin to $52 After Addition of BMN-701 to Model
Street Insider
Sun, 07/15/12 - 12:02 pm
BMN-701
Biomarin
Pompe disease
Genzyme pumps up Pompe meds; Fabrazyme still short
Fierce Pharma
Thu, 01/20/11 - 11:23 am
Genzyme
Pompe disease
Fabrazyme
Myozyme
Lumizyme
BioMarin's Pompe disease drug gets orphan status
Yahoo/AP
Mon, 08/30/10 - 12:22 pm
Biomarin
Pompe disease
orphan drugs
Genzyme Jumps on FDA Settlement, Approval of Pompe Remedy
Barron's
Tue, 05/25/10 - 05:10 pm
Genzyme
FDA
Pompe disease
Lumizyme
Genzyme eyes FDA ruling on Pompe drug
Bizjournals.com
Fri, 01/22/10 - 10:07 am
FDA
Pompe disease
Genzyme
Genzyme: Positive Development on the Lumizyme Front
Seeking Alpha
Thu, 12/3/09 - 07:31 pm
Lumizyme
Genzyme
Pompe disease
Genzyme Drops Kidney-Drug Plans Amid Pileup of Bad News
WSJ Online
Thu, 11/19/09 - 10:24 am
Pompe disease
Genzyme
Genzyme plans new Lumizyme application in weeks
Yahoo/AP
Wed, 05/6/09 - 06:13 pm
Genzyme
Lumizyme
Pompe disease
Drug Delay Hurts Genzyme
Yahoo/Zacks.com
Wed, 03/4/09 - 11:19 am
Genzyme
Pompe disease
Lumizyme

Pages