Friedreich's Ataxia

PTC's plans crash into regulatory reality as FDA demands data on 2 candidates, delaying filing
Fierce Biotech
Fri, 10/27/23 - 11:49 am
PTC Therapeutics
FDA
Friedreich's Ataxia
Biogen to acquire rare disease drugmaker Reata for $7.3B
BioPharma Dive
Fri, 07/28/23 - 11:50 am
Biogen
Reata Pharmaceuticals
M&A
Friedreich's Ataxia
PTC Cuts Early-Stage Pipeline but Pushes Forward on FA Drug After Phase III Flop
BioSpace
Wed, 05/24/23 - 06:42 pm
PTC Therapeutics
Friedreich's Ataxia
clinical trials
vatiquinone
FDA Approves First Therapy for Friedreich's Ataxia
BioSpace
Tue, 02/28/23 - 10:48 pm
Reata Pharmaceuticals
FDA
Friedreich's Ataxia
FDA scraps AdComm for Reata's rare disease candidate, leaving analysts squinting at the tea leaves
Fierce Biotech
Sun, 10/16/22 - 05:17 pm
Reata Pharmaceuticals
omaveloxolone
FDA
Friedreich's Ataxia
Larimar to respond to FDA this quarter on 15-month clinical hold of PhI Friedreich's ataxia drug
Endpoints
Fri, 08/12/22 - 10:23 am
Larimar Therapeutics
CTI-1601
clinical trials
FDA
Friedreich's Ataxia
Reata’s ‘regulatory concerns’ turn into three-month delay on FDA decision for Friedreich’s ataxia drug
Endpoints
Tue, 08/9/22 - 10:27 am
Reata Pharmaceuticals
Friedreich's Ataxia
FDA
omaveloxolone
Larimar kept in limbo as FDA maintains clinical hold on leading candidate
Fierce Biotech
Tue, 02/15/22 - 10:21 am
Larimar Therapeutics
Friedreich's Ataxia
FDA
clinical hold
CTI-1601
FDA places clinical hold on Larimar’s rare disease drug after deaths in monkey study
MedCity News
Wed, 05/26/21 - 11:36 pm
Larimar
clinical trials
Friedreich's Ataxia
FDA
clinical hold
Healx deploys its AI in hunt for Friedreich’s ataxia therapies
Pharmaforum
Fri, 04/9/21 - 10:49 am
Healx
artificial intelligence
Friedreich's Ataxia
Reata Pharmaceuticals Sees Hiccup in Filing for Approval of FA Drug
BioSpace
Wed, 08/12/20 - 12:11 am
Reata Pharmaceuticals
Friedreich's Ataxia
omaveloxolone
Reata shocks analysts with pivotal win in Friedreich's ataxia
Fierce Biotech
Tue, 10/15/19 - 10:18 am
Reata Pharmaceuticals
omaveloxolone
Friedreich's Ataxia
clinical trials
Reata gets another shot in Friedreich’s ataxia
EP Vantage
Wed, 08/7/19 - 10:50 am
Reata Pharmaceuticals
omaveloxolone
Friedreich's Ataxia
RegenxBio and Pfizer Partner on Gene Therapy for Friedreich's Ataxia
BioSpace
Wed, 07/31/19 - 11:50 pm
Regenxbio
Pfizer
gene therapy
Friedreich's Ataxia
ViroPharma pays Intellect Neurosciences $6.5 million for drug molecule rights
Yahoo/AP
Fri, 09/30/11 - 11:10 am
ViroPharma
Intellect Neurosciences
Friedreich's Ataxia
OX1