Vertex Receives Positive Opinion from CHMP for Kalydeco in Patients 12 to 24 months wth Cystic Fibrosis

Vertex Pharmaceuticals (Europe) announced on 10/19/18 that the European Medicines Agency’s (EMA) Committee for Medicinal Products for Human Use (CHMP) adopted a positive opinion for KALYDECO®(ivacaftor) to include the treatment of people with cystic fibrosis (CF) aged 12 to <24 months who have at least one of the following nine mutations in their cystic fibrosis transmembrane conductance regulator (CFTR) gene: G551D, G1244E, G1349D, G178R, G551S, S1251N, S1255P, S549N or S549R.