Takeda touts interim PhIII data of enzyme replacement therapy for rare blood disease

Takeda touts interim PhIII data of enzyme replacement therapy for rare blood disease

Source: 
Endpoints
snippet: 

Takeda says in an interim Phase III analysis that its enzyme replacement therapy reduced instances of low blood platelet count for patients with a rare blood clot disorder known as congenital thrombotic thrombocytopenic purpura (cTTP) compared to standard of care plasma-based therapies.