Novartis' Fabhalta is first FDA-approved therapy for rare disease C3G

Novartis' Fabhalta is first FDA-approved therapy for rare disease C3G

Source: 
Pharmaphorum
snippet: 

Novartis has a third FDA-approved indication for its oral therapy for complement-mediated diseases – Fabhalta – after getting a green light in ultra-rare kidney disease C3 glomerulopathy (C3G).