Leveraging tRNA to Scale Genetic Medicines for Rare Diseases and Beyond

The success and rapid evolution of the messenger RNA COVID-19 vaccines and the impact of FDA-approved small interfering RNA medicines like Onpattro are clear indications that the era of RNA-based medicines is well upon us. The sequence specificity of these products goes a long way to providing highly effective therapy against a variety of diseases while also reducing the safety risks associated with small molecule drugs.