Agios wins FDA approval for drug to treat rare form of anemia

Agios wins FDA approval for drug to treat rare form of anemia

Source: 
Stat
snippet: 

The Agios drug, mitapivat, is the first approved treatment for pyruvate kinase deficiency, a rare, inherited disorder that results in the rapid destruction of red blood cells. Given as a pill, mitapivat is designed to activate an enzyme called pyruvate kinase-R that red blood cells use to convert sugars into energy.