From no drugs to 3: Patients with spinal muscular atrophy now face hard choices

From no drugs to 3: Patients with spinal muscular atrophy now face hard choices

Source: 
BioPharma Dive
snippet: 

Since 2016, three drugs have been approved to slow or stop the disease, from the most severe "Type 1" form that typically leads to death by age two to the more mild forms, like Broadhurst's, that can rob people of the ability to walk or swallow.