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Roche’s Evrysdi offers sustained benefits in SMA extension trial in children

cafead

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  • cafead   Jun 10, 2024 at 11:12: AM
via Roche has announced five-year findings from the open-label extension portion of the FIREFISH study, where Evrysdi (risdiplam) offered sustained efficacy and safety in children with type 1 spinal muscular atrophy (SMA).

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