- cafead   Jul 03, 2023 at 11:42: AM
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- Data from ongoing FIREFISH study confirm long-term efficacy and safety profile of Evrysdi in children with Type 1 SMA
- Ninety-one percent of children were alive at month 48
- More than 95% maintained the ability to swallow - without treatment they would have required feeding support and majority would have died within 2 years
- Evrysdi is now approved in 99 countries with more than 8,500 patients treated globally
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