• Make it like cafepharma, but for different industries: over the years we’ve had suggestions for creating a site similar to cafepharma, but for different industries. Now there is a place. Check out CompanyUnderground for company forums in other industries. Don’t see a company? Request it here. Let your friends and family outside the pharma/medical sales space know they now have a safe, anonymous place to talk.


FDA Approves Mirum Pharmaceuticals' Drug As First For Genetic Disorder With Inability To Break-Down Cholesterol

Quote
cafead

cafead

Administrator
Staff member
  • cafead   Feb 23, 2025 at 10:52: PM
via
  • FDA approves Mirum's Ctexli, the first treatment for cerebrotendinous xanthomatosis, a rare genetic disorder affecting fat metabolism.
  • In a trial, Ctexli significantly reduced cholesterol metabolites linked to CTX, but it carries a liver toxicity warning requiring monitoring

article source
 






Top Bottom
Back
Quote