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orphan drugs

Failed as a Cancer Treatment - Selumetinib Granted Orphan Designation in Europe for Neurofibromatosis Type 1

Failed as a Cancer Treatment - Selumetinib Granted Orphan Designation in Europe for Neurofibromatosis Type 1

CP Wire

Array Biopharma

neurofibromatosis

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FDA Finalizes Guidance Closing Pediatric Study Loophole

FDA Finalizes Guidance Closing Pediatric Study Loophole

RAPS.org

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Inozyme Pharma Receives Orphan Drug Designation for INZ-701 in the United States and European Union

Inozyme Pharma Receives Orphan Drug Designation for INZ-701 in the United States and European Union

CP Wire

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Seattle Genetics Announces Results of Two Ph II Trials of Tucatinib in HER2- Positive Metastatic Breast Cancer

Seattle Genetics Announces Results of Two Ph II Trials of Tucatinib in HER2- Positive Metastatic Breast Cancer

CP Wire

Seattle Genetics

clinical trials

HER2-positive metastatic breast cancer

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Tetra Discovery Partners Initiates Ph II Trial of Fragile X Syndrome Drug

Tetra Discovery Partners Initiates Ph II Trial of Fragile X Syndrome Drug

CP Wire

Tetra Discovery Partners

Fragile X syndrome

clinical trials

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Eagle Receives Orphan Drug Designation for Bendeka

Eagle Receives Orphan Drug Designation for Bendeka

CP Wire

Eagle Pharmaceuticals

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Are Orphan Drugs Getting Too Much Attention By Payers And Policymakers?

Are Orphan Drugs Getting Too Much Attention By Payers And Policymakers?

Forbes

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5 Best-Selling Orphan Drugs in the U.S.

5 Best-Selling Orphan Drugs in the U.S.

Motley Fool

Teva Pharmaceutical

Bristol-Myers Squibb

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Half of orphan drug sales to come from cancer, Evaluate finds

Half of orphan drug sales to come from cancer, Evaluate finds

Biopharma Dive

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Orphan drugs to grow twice as fast as rest of the industry: report

Orphan drugs to grow twice as fast as rest of the industry: report

Medical Marketing and Media

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Market Exclusivity is not What Attracts Orphan Drug Investment, Research Finds

Market Exclusivity is not What Attracts Orphan Drug Investment, Research Finds

RAPS.org

market exclusivity

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Eloxx Receives Another Orphan-Drug Designation for ELX-02

Eloxx Receives Another Orphan-Drug Designation for ELX-02

CP Wire

Eloxx Pharmaceuticals

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EU Advisory Group Backs Orphan Drug Designation for Alnylam's ALN-TTRsc02 for ATTR Amyloidosis

EU Advisory Group Backs Orphan Drug Designation for Alnylam's ALN-TTRsc02 for ATTR Amyloidosis

CP Wire

ATTR amyloidosis

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No slowing down: Orphan drug designations skyrocket in 2017

No slowing down: Orphan drug designations skyrocket in 2017

Medical Marketing and Media

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Analyzing the orphan drugs market ($127bn)

Analyzing the orphan drugs market ($127bn)

GoinPharma

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FDA to Launch New Pilot Program for Orphan Designation Requests

FDA to Launch New Pilot Program for Orphan Designation Requests

RAPS.org

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Despite increased spending, orphan drugs still small piece of US medicines market

Despite increased spending, orphan drugs still small piece of US medicines market

Biopharma Dive

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FDA is Advancing the Goals of the Orphan Drug Act

FDA is Advancing the Goals of the Orphan Drug Act

FDA Voice

Orphan Drug Act

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FDA Determines that Deuterated Compounds are NCEs and Different Orphan Drugs Versus Non-deuterated Versions

FDA Determines that Deuterated Compounds are NCEs and Different Orphan Drugs Versus Non-deuterated Versions

FDA Law Blog

deuterated drugs

Teva Pharmaceutical

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FDA Plots Elimination of the Orphan Drug Designation Request Backlog

FDA Plots Elimination of the Orphan Drug Designation Request Backlog

RAPS.org

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